SGT-003 Granted Orphan Drug Designation for Duchenne Muscular Dystrophy (DMD)

The research landscape for Duchenne muscular dystrophy (DMD) has been steadily increasing. Researchers are exploring more therapies, including gene therapies, that could transform the lives of those with this rare…

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New Podcast Episode: The Intersection of Motherhood and Chronic Illness feat. aHUS Patient Advocate Taylor Coffman
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New Podcast Episode: The Intersection of Motherhood and Chronic Illness feat. aHUS Patient Advocate Taylor Coffman

We are excited to announce that Patient Worthy's award-winning podcast "Wait, How Do You Spell That? A Rare Disease Podcast" is back with a new episode. This week, Colby is…

Continue Reading New Podcast Episode: The Intersection of Motherhood and Chronic Illness feat. aHUS Patient Advocate Taylor Coffman