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Daily Archives: March 4, 2024

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Rethinking Clinical Trials for Rare Disease Gene Therapies
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Rethinking Clinical Trials for Rare Disease Gene Therapies

  • Post author:James Moore
  • Post published:March 4, 2024
  • Post category:Rare Disease

According to a story from BioSpace, the current standard approaches for drug development aren't well suited for rare diseases, which have unique characteristics in comparison to more widespread illnesses. As…

Continue Reading Rethinking Clinical Trials for Rare Disease Gene Therapies
ICYMI: OLUMIANT Now Approved in Canada for Alopecia Areata
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ICYMI: OLUMIANT Now Approved in Canada for Alopecia Areata

  • Post author:Jessica Lynn
  • Post published:March 4, 2024
  • Post category:Alopecia areata

At the end of January 2024, global healthcare leader Eli Lilly and Company shared that its therapy OLUMIANT (baricitinib) received regulatory approval in Canada for the treatment of severe alopecia…

Continue Reading ICYMI: OLUMIANT Now Approved in Canada for Alopecia Areata
WORLDSymposium: Nexviazyme Improves Ptosis in Infantile-Onset Pompe Disease
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WORLDSymposium: Nexviazyme Improves Ptosis in Infantile-Onset Pompe Disease

  • Post author:Jessica Lynn
  • Post published:March 4, 2024
  • Post category:Pompe Disease

The 20th annual WORLDSymposium took place from February 4-9, 2024. During the course of the research conference, at least one presentation centered on data from the Phase 2 Mini-COMET long-term…

Continue Reading WORLDSymposium: Nexviazyme Improves Ptosis in Infantile-Onset Pompe Disease

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