Novartis has announced encouraging results from two pivotal studies involving its experimental drug, ianalumab, targeting two different autoimmune indications. As reported by BioPharma Dive, the Swiss pharmaceutical company revealed positive data…
Vepdegestrant, an investigational oral selective estrogen receptor degrader (SERD), has reached a critical milestone as the U.S. Food and Drug Administration (FDA) reviews its New Drug Application (NDA) for use…
Millions of social media posts and billions of views have turned TikTok into an influential platform for mental health conversations, but experts warn that using the app to self-diagnose can…
Recent advancements in the treatment of metastatic urothelial cancer (mUC) have dramatically improved patient outcomes, primarily due to the introduction of antibody-drug conjugates (ADCs) and immune checkpoint inhibitors (ICIs). According…
AstraZeneca, a global leader in pharmaceuticals, has taken a significant step into the rare disease arena in South Africa, aiming to improve diagnosis, treatment, and support for patients facing these…
Sanofi has announced a significant regulatory milestone for its investigational therapy SAR446523, a monoclonal antibody targeting GPRC5D, after the U.S. Food and Drug Administration (FDA) granted it orphan drug designation…
Australian athlete Tiana Death has bravely shared her journey after being struck by autoimmune encephalitis, a rare and serious brain disease that upended her life and forced her to relearn…
The U.S. Food and Drug Administration (FDA) has broadened the approval of Empaveli (pegcetacoplan), a complement inhibitor, to include the treatment of two rare and serious kidney diseases: C3 glomerulopathy…
In a significant advancement for cancer treatment, the U.S. Food and Drug Administration (FDA) has granted accelerated approval to Bavencio (avelumab) for the treatment of patients with locally advanced or…
In Chapel Hill, North Carolina, a family’s life changed dramatically when their young twin daughters were diagnosed with Batten disease, a rare and devastating genetic disorder. According to MSN.com, the…
Biogen has achieved a significant regulatory milestone with the UK Medicines and Healthcare products Regulatory Agency (MHRA) granting approval for Qalsody (tofersen), a treatment specifically developed for a rare and…
Sydney health authorities are responding to a rare disease outbreak after a confirmed case of melioidosis resulted in one death. The incident, reported by MSN.com, has brought the little-known but…
A growing body of evidence suggests that GLP-1 receptor agonists, a class of medications commonly used to treat diabetes and obesity, may play an important role in managing hidradenitis suppurativa…
A recent study has unveiled a novel treatment that could significantly lessen brain damage following a stroke, offering hope for more effective therapies in the future. According to World Pharma…
Inflammatory bowel disease (IBD), which includes Crohn’s disease and ulcerative colitis, is a lifelong condition that disrupts the gastrointestinal tract and significantly impacts quality of life. While IBD has no…
Calidi Biotherapeutics has achieved a significant milestone with the U.S. Food and Drug Administration (FDA) granting Fast Track designation to its experimental therapy, CLD-201 SuperNova, for the treatment of glioblastoma.…
A recent study has revealed encouraging results for mirikizumab, an investigational monoclonal antibody, in addressing one of the most distressing symptoms of Crohn’s disease: bowel urgency. According to Medscape, this…
AbbVie, a global biopharmaceutical leader, has reported disappointing results from a phase 2 clinical trial evaluating its interleukin-1 (IL-1) targeting drug, ABBV-668, as a monotherapy for patients with moderate to…
A new Missouri law is shining a spotlight on the vital need for awareness of rare childhood diseases, thanks in large part to the advocacy efforts of a Eureka, Missouri…
Microbiotica, a UK-based biotechnology company focused on developing microbiome-based therapeutics, has reached a significant milestone by completing patient recruitment for its phase 1b clinical trial in ulcerative colitis (UC). According…
A recent study highlighted by World Pharma News reveals that maintaining a healthy diet can significantly slow the progression of chronic diseases among older adults. Chronic diseases—such as diabetes, heart…
In our second installment from our series of reports provided by our partner TREND Community, we are going to be focusing on a different condition over the next four weeks. …
Serina Therapeutics, a clinical-stage biotechnology company, has announced a major development in the treatment of Tardive Dyskinesia (TD) by advancing its innovative POZ-VMAT2i candidate into clinical development. This move, reported…
Immunotherapy, once considered a niche treatment, has rapidly become a central pillar in the fight against cancer. As detailed in a recent article from Becker’s Hospital Review, this innovative approach…
Researchers have unveiled a groundbreaking laboratory model that could transform the search for new therapies against an aggressive and often lethal blood cancer: acute myeloid leukemia (AML). AML is notorious…
© Copyright 2024 Patient Worthy
Sign Up With a Patient Worthy Account and Share Your Rare Story
- OR -
Make a difference, share your experiences and get paid. Opt-in and join Patient Worthy's panel for paid opportunities such as surveys, market research, patient advisory panels and more.
- OR -
Make a difference, share your experiences and get paid. Opt-in and join Patient Worthy's panel for paid opportunities such as surveys, market research, patient advisory panels and more.
