Rose became acquainted with Patient Worthy after her husband was diagnosed with Acute Myeloid Leukemia (AML) six years ago. During this period of partial remission, Rose researched investigational drugs to be prepared in the event of a relapse. Her husband died February 12, 2021 with a rare and unexplained occurrence of liver cancer possibly unrelated to AML.
Continued From Part One Multiple myeloma is caused by the buildup of abnormal white blood cells that form tumors found primarily in bones. Available treatments work for short periods…
Globe Newswire recently published an article announcing positive results from Amolyt Pharma’s Phase IIa proof of concept clinical trial of AZP-3601. Amolyt Pharma, Cambridge, Massachusetts, and Lyon, France, is a…
Part 1 Newswise recently published exciting news of a therapy that causes the immune system to destroy cancer cells in the bone marrow. Researchers at Icahn School’s Tisch Cancer Center…
Waldenstrom macroglobulinemia (WM) is defined as a B-cell lymphoplasmacytic lymphoma. Data from patients in Latin America on WM are scarce. Researchers are hoping to fill the void by analyzing…
The latest statistics on heart disease and its effect on Black communities are startling. According to an article in the Dallas Examiner, Black people are fifty to seventy percent more…
A team of researchers at Shanghai’s Fudan University, acting upon the knowledge that ketogenic diets can boost liver ketone production, have recently examined the possibility of preventing thrombocytopenia (low…
Do you wish to be heard? Recently PR Newswire announced that on the 28th of February 2023, NORD and the worldwide community of rare disorders will be raising awareness…
Contrary to simply stopping tumor growth, the biomedical engineers at Duke University have successfully demonstrated a new treatment for pancreatic cancer in a mouse model that may make a…
Med City News published an article by Bruce Feinberg, M.D. at Cardinal Heath, examining CAR-T treatments and the impact they have had in medicine during the past five years. CAR-T's…
Editor's Note: Chronic conditions and rare diseases don't discriminate, Patient Worthy and its partners are interested in amplifying the voices of those from all identities and backgrounds. If you have…
In 2021, Alyssa, who is now thirteen years old, and her family were told that she had acute lymphoblastic leukemia. Alyssa did not respond to either the standard leukemia…
According to a recent article featured in Biospace, researchers found substantial evidence of a biochemical correction after treating an eleven-year girl for Gaucher Disease. This is the first pediatric case…
Compassion [kuhm-pash-uhn] noun A feeling of deep sympathy and sorrow for another who is stricken by misfortune, accompanied by a strong desire to alleviate the suffering. Compassion Corner is a…
Researchers at Brown University, in collaboration with an MIT research team, discovered a method of penetrating the blood-brain barrier (BBB) in mice and delivering medication to treat lethal tumors…
Have you ever wondered how a rare disease can take control of a person’s life? The deteriorating health, being unable to receive an accurate diagnosis, and more importantly finding an…
Genetech recently announced the FDA’s approval of Tecentriq to treat alveolar soft part sarcoma (ASPS) pediatric and adult patients over the age of two. This first-ever treatment has been developed…
An announcement via PR NewsWire by NeuroSense Therapeutics based in Cambridge, Massachusetts carried the results of its multi-dose study of PrimeC to treat amyotrophic lateral sclerosis (ALS) Expectations are…
When we look at statistics that show thirty million people in the U.S. has one of seven thousand rare diseases, they may not seem rare. However, when we realize that…
The CDC lists lung cancer as the third most common type of cancer in the United States with the highest death rate. Estimates are given of 2.2 million patients worldwide…
Medscape Medical News reports that results have been received from the OCCLURANDOM Phase 2 trial which is the first randomized trial investigating the antitumor effect of the peptide receptor radionuclide…
Dr. Jose Sandoval-Sus, an oncologist at the Moffitt Cancer Center, was recently interviewed with Medscape regarding his review which was published in the October 2022 Current Oncology Reports. The new…
Inside Precision Medicine recently featured an article focusing on biomarkers that suggest the likelihood of drugs called checkpoint inhibitors to “backfire” during melanoma treatment. Checkpoint inhibitors are one of the…
Previous research presents strong evidence favoring shared decision-making after a medical diagnosis. One major improvement has been designing treatment plans that include a good deal of the patient’s goals and…
The loss of axons (nervous system wiring) has been responsible for various neurodegenerative diseases such as peripheral neuropathies, Parkinson’s disease, glaucoma, and amyotrophic lateral sclerosis (ALS). According to a…
In the ongoing search for prevention and a cure for Alzheimer’s Disease (AD), a study was conducted at Colorado’s Anschutz Medical Campus. The researchers found that memory and learning are…
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