Rose became acquainted with Patient Worthy after her husband was diagnosed with Acute Myeloid Leukemia (AML) six years ago. During this period of partial remission, Rose researched investigational drugs to be prepared in the event of a relapse. Her husband died February 12, 2021 with a rare and unexplained occurrence of liver cancer possibly unrelated to AML.
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Health professionals continually warn the public to take steps to guard against sunburn. We often hear the expression “one in a million.” The phrase and the warning truly pertain…
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Mother Hosts Moonlight Ball to Help Her Daughter with Xeroderma Pigmentosum
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Roche has added another failure this year with its drug gantenerumab. As noted in Fierce Biotech, the drug was unable to improve functional or cognitive decline in two Phase…
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Alzheimer’s: Another Drug Failure Has the Researchers Questioning the Science
Two emergency surgeries that began 48 hours after birth, meningitis, and over a month in the intensive care units of three Seattle hospitals prompted Layla Babayev’s desperate parents to enroll…
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Whole Genome Sequencing May Have Saved This Baby’s Life
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Prior to the FDA’s approval this month, nirogacestat (Ogsiveo) received the following FDA designations applicable to the treatment of desmoid tumors: Breakthrough therapy providing a rapid review. Fast track to…
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Springworks Wins FDA Approval for Nirogacestat to Treat Desmoid Tumors
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Meenakshi Rao, an assistant pediatric professor at the Children’s Hospital in Boston, recently expressed his opinion to the RNA-Seq blog that inflammation, not bacteria, should be targeted, as infections…
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C. Diff: Professors Suggest Inflammation, Not Bacteria Should be Targeted
445 words 10% matched vs. 2061 words 2% matched We invented medicines to kill bacteria; now, the bacteria are killing us. Lucien Swetschinski, a researcher and co-author at IHME, told…
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Experts Are Comparing the Threat of Bacterial Antimicrobial Resistance (AMR) to the HIV/AIDS Health Crisis
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Josie Lawrence, a 42-year-old comedian and actress residing in East London, UK, has adopted an unconventional training routine for her even more extraordinary walk along the Great Chinese Wall,…
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Comedian and Actress Trained for Charity Walk after Deep Cartilage Knee Damage
Editor's Note: We believe that patients are a key part of developing and leading the conversation in disease communities. Patient Worthy sometimes partners with reputable agencies that wish to speak…
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Study: The Effect of Patient Support Groups on Pulmonary Hypertension Patients and their Caregivers
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The goal of providing precision techniques to cancer care is becoming increasingly complicated. According to a recent article in Inside Precision Medicine, the cause may be attributed to the…
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Using AI Software to Support Clinical Decisions in Cancer Treatment
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The FDA has granted IDEAYA Biosciences fast track status for IDE161 as a treatment for HR+, Her2- breast cancer. The therapy is a selective inhibitor of ADP ribose glycohydrolase…
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IDEAYA’s IDE161 Receives Fast Track Designation for HR+ Her2- Breast Cancer
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The need for increased awareness about Alzheimer’s disease is growing. The number of Alzheimer’s patients has increased since 1983, the year President Reagan designated November as Alzheimer’s Disease Awareness…
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November was Alzheimer’s Awareness Month
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CRISPR was first described ten years ago as a viral mechanism for defense, taken from bacteria, which could be transformed into genetic scissors and accurately alter DNA. About Casgevy CRISPR…
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U.K. Health Authorities Grant Approval for a New Medicine using CRISPR Gene Editing to Treat Beta thalassemia and Sickle Cell
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Patients with severe asthma with an eosinophilic phenotype who are 12 years of age or older may now receive treatment with FASENRA as an add-on maintenance treatment. Note that…
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Phase III Trial meets Primary Endpoint for Patients with Eosinophilic Granulomatosis with Polyangiitis (EGPA)
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Vamorolone, now marketed as AGAMREE®, is termed a dissociative steroid therapy, as it has proven its potential to retain the muscle-strengthening and anti-inflammatory benefits of corticosteroids. On the other side…
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Vamorolone Has Been FDA Approved to Treat Duchenne Muscular Dystrophy
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In December 2019, three months after his retirement, Paul Goodfellow received a diagnosis of invasive cancer of the bladder. He received three cycles of chemotherapy and then major surgery that…
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Combo Treatment in Clinical Trial Doubles Metastatic Bladder Cancer Survival
In the year 2000, the number of Dengue cases was reported to be approximately one-half million. In October 2023 the total reached 4.2 million cases of Dengue virus. The virus…
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As Temperatures Rise, Dengue Fever is Spreading. Can it be Stopped?
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Every three to four minutes, someone in the U.S. is diagnosed with a blood disease such as lymphoma, leukemia, or sickle cell anemia. As reported in the Pittsburgh Post-Gazette,…
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Mom Signed Up Thousands of Stem Cell Donors in Support of Son with IPEX
The words ‘vigorous exercise’ usually bring to mind running marathons or playing pickleball. Inside Precision Medicine reports that researchers at a Sydney, Australia University tracked the daily activity of more…
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Study Shows an Average of 4 1/2 Minutes of Vigorous Exercise May Reduce the Risk of Cancer by 32%
Chip Wilson, billionaire founder of Lululemon Athletica, was first diagnosed with muscular dystrophy in 1987 at the age of 32. Wilson, who is now 66 years old told Global…
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Wealthy Facioscapulohumeral Muscular Dystrophy Patient Invests $100 Million to Find a Cure
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Arcus Biosciences and Gilead Sciences issued a press release announcing encouraging overall response rates and six-month progression-free survival rate for their combination treatment of domvanalimab plus zimberelimab and chemotherapy…
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Encouraging Findings in Phase 2 Gastric Cancer Clinical Trial
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Cancer immunotherapy has transformed the landscape of cancer treatment, revealing that not all patients with solid tumors respond effectively to this approach. As reported by News Medical Life Sciences,…
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Nanocapsules Enhance Immune Response Against Cancer Tumors
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An individual has a good chance of recovering from an injury to his or her legs or arms, but it is not always the case when the injury involves…
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Scientists Find Biomarker for Predicting Neuron Repair, with Implications for Future Therapies
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Scientists have previously suggested that the gut microbiome plays a role in causing Alzheimer’s disease, and this has now been confirmed. A recent report from ScienceAlert covered a study…
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Scientists Demonstrate Gut Microbiome Connection with Transfer of Alzheimer’s to Healthy Animals
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Professionals from all corners of the world convene at SSIEM each year to discuss the latest groundbreaking discoveries. According to a report in BioSpace, one such breakthrough was presented by…
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Promising Interim Data in Phase 1/2 Hunter Syndrome Trial
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If Wave Life Sciences’ recently submitted trial application for WVE-006 is approved, it will become the first RNA editing treatment in a clinical development setting. Wave’s CEO, Paul Bolno,…
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Wave Life Science’s New Trial Application is Causing Renewed Excitement Around RNA Editing