As reported in Crwe World; the biopharmaceutical company Chiasma aims to create oral consumed therapies in order to provide acromegaly patients who have a chronic need for injections with an…
According to the Parkinson’s News Today; in the UK, NRG Therapeutics has been awarded £1 million (about $1.3 million) to continue advancing their studies on the mitochondria responsible for producing…
In a story reported in News Medical Life Sciences, researchers attempting to treat rare diseases often find themselves with a dilemma- while there aren’t many patients to test treatments on in…
As reported in Parkinson's News Today, three research teams are set to dig deeper into developing a potential diagnostic tool to diagnose Parkinson’s- an opportunity awarded in the form of…
As reported by the National Hemophilia Foundation, researchers are seeking to understand what patients with chronic pain need and want, so as to make treatment safer and more effective. In…
As published by the Food and Drug Administration; The U.S. FDA has just approved the first FDA approved therapy derived from cannabis (Epidiolex, a CBD solution) to treat tuberous sclerosis…
When Trey Kearns was two, he had a terrible itch. His itch wasn’t like yours - it was inside the body, meaning it's an itch you can’t scratch. They came…
As reported in Parkinson's News Today, a new study published in Family Medicine and Community Health has looked into the relationship between concussions and certain other neurological disorders that patients have…
As reported in Parkinson's News Today; Daniel Vesely had a hunch. He had been using mannitol, an easy to access over-the-counter sweetener and supplement often used by people with diabetes,…
As reported in Medical Xpress, researchers are studying how patients using bisphosophonates as part of a treatment regime to avoid fractures associated from osteoporosis are affected by "drug holidays" when…
As reported in Disability Horizons, the coronavirus has brought aspects of health and safety into the view for many citizens who had never had to be particularly considerate or careful…
In a new article in the journal Science Advances, neuroscientists have found a specific mechanism that is responsible for the familial migraines. A type of brain cell called astrocytes have…
In a study published in BMC Pediatrics, researchers have found atypical hemolytic uremic syndrome (aHUS) and autoimmune thyroid disease may not only be a relatively common pair of rare diseases…
As reported in Parkinson's News Today, an investigational therapy to treat patients with Alzheimer's disease and Parkinson’s disease has had its Phase 2 trial approved by the central institutional review…
As reported in Parkinson's News Today, three nurses have been awarded $10,000 by The Parkinson’s Foundation to carry out local projects for Parkinson’s patients to better their experience. Each of…
As COVID-19 grips the world, scientists are chasing after it to find the full spectrum of effects as it interacts with human biochemistry. While known for its characteristic cough and…
As reported in Michael J. Fox News, the FDA has just approved the novel Percept PC Neurostimulator, a device inserted into the brain of patients with Parkinson's to administer deep…
David Fajgenbaum toes the line between patient and doctor. After growing up with a physician as a father, Fajgenbaum chose to follow in his footsteps. His most important lessons came…
A cannabinoid medication that uses a non-psychoactive ingredient of cannabis to treat rare forms of epilepsy has now been recategorized as a schedule 5 drug in the UK, the least…
A study in the Journal of Movement Disorders on patients with Parkinson's disease has found a relationship between sedentary living and attention difficulty. Exercise is the age old medicine, with…
Emily Ventura was already well aware of the risk of germs before coronavirus. She works as a nurse in the ICU and takes care of her 8-year-old, who is immunosuppressed.…
As reported in Business Fortnight, the top level gene therapy company AVROBIO has announced successful clinical trials for investigational drugs for Fabry disease and cystinosis. The CEO of AVROBIO, Geoff…
As reported in BioSpace; the US Food and Drug Administration (FDA) has granted breakthrough therapy designation, an expedited drug review, to brensocatib, a novel drug to treat non-cystic fibrosis bronchiectasis…
In the United States of Care, Catherine Jacobson tells her story of being born in South Korea with OCA1A albinism which caused her to be legally blind, being adopted by…
As reported in Globe News Wire, amidst a difficult time for rare disease patients as the medical world’s refocuses on the coronavirus, a new scholarship has been announced that could…
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