Patients with Newly Diagnosed Fanconi Anemia Should Avoid alloHSCT

A study in the American Journal of Hematology recently presented some troubling findings on the relationship between Fanconi anemia and allogeneic hematopoietic stem cell transplantation (alloHSCT). Patients who participated in alloHSCT before achieving…

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Experimental Gene Therapy for Fanconi Anemia Earns Fast Track and Regenerative Medicine Advanced Therapy Designation

According to a story from BioPortfolio, the gene therapy company Rocket Pharmaceuticals has recently announced that the company's investigational gene therapy RP-L102 has earned both Fast Track and Regenerative Medicine…

Continue Reading Experimental Gene Therapy for Fanconi Anemia Earns Fast Track and Regenerative Medicine Advanced Therapy Designation
Gene Therapy for Fanconi Anemia Gains IND Clearance From the FDA
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Gene Therapy for Fanconi Anemia Gains IND Clearance From the FDA

According to a story from BioSpace, the gene therapy company Rocket Pharma recently announced that its investigational product candidate RP-L102 recently saw its Investigational New Drug (IND) application gain approval…

Continue Reading Gene Therapy for Fanconi Anemia Gains IND Clearance From the FDA