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Sanofi’s Gene Therapy for Wet AMD Earns FDA Fast Track Designation

Sanofi’s Gene Therapy for Wet AMD Earns FDA Fast Track Designation

  • Post author:Austin Newman
  • Post published:October 19, 2025
  • Post category:Macular degeneration

The U.S. Food and Drug Administration (FDA) has granted Fast Track designation to SAR402663, Sanofi’s investigational gene therapy for neovascular age-related macular degeneration (AMD). As seen in a report, this…

Continue Reading Sanofi’s Gene Therapy for Wet AMD Earns FDA Fast Track Designation
First Patient Dosed in Clinical Trial for Promising Dry AMD Therapy PST-611

First Patient Dosed in Clinical Trial for Promising Dry AMD Therapy PST-611

  • Post author:Bree Clare
  • Post published:July 13, 2025
  • Post category:Macular degeneration

A new milestone has been reached in the search for effective treatments for dry age-related macular degeneration (AMD), as the first patient has now been dosed in a clinical trial…

Continue Reading First Patient Dosed in Clinical Trial for Promising Dry AMD Therapy PST-611
Gene Therapy for Wet AMD Begins Dosing in Cohort 4 of Trial
source: pixabay.com

Gene Therapy for Wet AMD Begins Dosing in Cohort 4 of Trial

  • Post author:Sunniva Bean
  • Post published:May 18, 2020
  • Post category:Wet macular degeneration

As reported in Biospace, Adverum Biotechnologies, a gene therapy company focused on clinical stage trials for rare and ocular diseases with unmet needs, has successfully dosed a patient in their…

Continue Reading Gene Therapy for Wet AMD Begins Dosing in Cohort 4 of Trial
Phase 1 Clinical Trial for Stargardt Disease to be Initiated Soon!

Phase 1 Clinical Trial for Stargardt Disease to be Initiated Soon!

  • Post author:Trudy Horsting
  • Post published:April 26, 2019
  • Post category:Stargardt Disease

Stargardt Disease Stargardt disease is a rare disease which results in progressive vision loss. It is also referred to as juvenile macular degeneration. Most often, the disease presents during childhood.…

Continue Reading Phase 1 Clinical Trial for Stargardt Disease to be Initiated Soon!
You Are Not Alone: Empowering the Advanced Kidney Cancer Community
Finding Light Through Story-The Power of Ambassadorship in the Endometrial Cancer Community
*cancer that cannot be removed with surgery or has spread to other parts of the body. GEJ= gastroesophageal junction (where the esophagus joins the stomach)
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