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Genethon Launches the First Clinical Trial for Crigler-Najjar Syndrome
source: pixabay.com

Genethon Launches the First Clinical Trial for Crigler-Najjar Syndrome

  • Post author:Rose Duesterwald
  • Post published:January 30, 2023
  • Post category:Crigler Najjar syndrome- type 2/Rare Disease

  Genethon is a non-profit organization committed to the design and development of gene therapies for rare diseases. This unique company is a pioneer in identifying genes relating to genetic…

Continue Reading Genethon Launches the First Clinical Trial for Crigler-Najjar Syndrome
This Grandfather Bikes to Raise Money for Held in Our Hearts
source: pixabay.com

This Grandfather Bikes to Raise Money for Held in Our Hearts

  • Post author:Kendall Mason
  • Post published:June 24, 2021
  • Post category:Congenital Nephrotic Syndrome

Mark Dalziel has big plans for this weekend; he's going to bike the length of Scotland within two days. He has a very good reason for doing so, which is…

Continue Reading This Grandfather Bikes to Raise Money for Held in Our Hearts
A Gene Therapy for Crigler-Najjar Syndrome is in Development
amorimbiotec / Pixabay

A Gene Therapy for Crigler-Najjar Syndrome is in Development

  • Post author:James Moore
  • Post published:March 8, 2019
  • Post category:Crigler Najjar syndrome- type 2/Rare Disease

According to a story from news-medical.net, a team of scientists associated with the CURECN project are starting to develop a gene therapy that has the potential to cure the rare…

Continue Reading A Gene Therapy for Crigler-Najjar Syndrome is in Development
3-Year-Old With Congenital Nephrotic Syndrome Receives Kidney
Source: Pixabay

3-Year-Old With Congenital Nephrotic Syndrome Receives Kidney

  • Post author:Meagan Fulps
  • Post published:February 26, 2018
  • Post category:Congenital Nephrotic Syndrome/Rare Disease

Ever since New Brunswick 3-year-old, Zaccari, was born, they knew he needed a new kidney. CTV News Atlantic originally reported that Zaccari was born with congenital nephrotic syndrome, a rare…

Continue Reading 3-Year-Old With Congenital Nephrotic Syndrome Receives Kidney
Finding Light Through Story-The Power of Ambassadorship in the Endometrial Cancer Community
*cancer that cannot be removed with surgery or has spread to other parts of the body. GEJ= gastroesophageal junction (where the esophagus joins the stomach)
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