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First-in-Human Study Shows Promise for Innovative Spray Gel in Treating Post-ESD Ulcers

First-in-Human Study Shows Promise for Innovative Spray Gel in Treating Post-ESD Ulcers

  • Post author:Bree Clare
  • Post published:July 3, 2025
  • Post category:Rare Disease

A groundbreaking clinical milestone has been reached in gastroenterology with the publication of a first-in-human study evaluating a novel spray gel for the treatment of ulcers following endoscopic submucosal dissection…

Continue Reading First-in-Human Study Shows Promise for Innovative Spray Gel in Treating Post-ESD Ulcers
Rare Disease Biotech Achieves Key Milestone with Promising Therapy for FPL

Rare Disease Biotech Achieves Key Milestone with Promising Therapy for FPL

  • Post author:Bree Clare
  • Post published:June 19, 2025
  • Post category:Familial Partial Lipodystrophy

A recent article from Pharmaceutical Manufacturer highlights a significant achievement in the rare disease sector, as Rare Disease Biotech announced reaching a major milestone in the development of its new…

Continue Reading Rare Disease Biotech Achieves Key Milestone with Promising Therapy for FPL
How Will New Treatment Make Life With IPF a Little Easier?
https://pixabay.com/en/rainbow-rain-arch-palmer-lake-436171/

How Will New Treatment Make Life With IPF a Little Easier?

  • Post author:James Ernest Cassady
  • Post published:August 23, 2016
  • Post category:IPF/Rare Disease/Timely

What does pulmonary fibrosis, or scarring of the lungs, have to do with blood? Probably more than I'm aware, because when I first saw that a biopharma company specializing in…

Continue Reading How Will New Treatment Make Life With IPF a Little Easier?
How The FDA Is Making This Boy More Sick

How The FDA Is Making This Boy More Sick

  • Post author:Erica Zahn
  • Post published:January 28, 2016
  • Post category:Cystic Fibrosis/Duchenne Muscular Dystrophy/Rare Disease

Last year, the FDA approved a record number of new drugs to treat rare diseases, according to the National Organization for Rare Disorders (NORD). In all, 21 "orphan" drugs were…

Continue Reading How The FDA Is Making This Boy More Sick
You Are Not Alone: Empowering the Advanced Kidney Cancer Community
Finding Light Through Story-The Power of Ambassadorship in the Endometrial Cancer Community
*cancer that cannot be removed with surgery or has spread to other parts of the body. GEJ= gastroesophageal junction (where the esophagus joins the stomach)
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