When it comes to rare diseases, many doctors simply just don't know the proper way to diagnose, monitor, and treat them. It's difficult to know how to respond to every…
In the past, treatment for progressive familial intrahepatic cholestasis (PFIC) was symptomatic or surgical, meaning that there weren't too many treatment options for this patient population. This all changed with…
While extremely rare, it is important to be prepared in case of vaccine-induced immune thrombocytopenia and thrombosis (VITT). This condition only occurs in 14.2 of every million COVID-19 vaccine doses,…
As seen in a press release by Bioindustry; the UK BioIndustry Association (BIA) has published findings from a survey on the public’s interest in supporting rare access to affordable medicine…
The National Institute for Health and Clinical Excellence (NICE), an agency under the UK's National Health Service (NHS), has recently rejected Zeposia. Zeposia is an oral, multiple sclerosis (MS) treatment…
As originally reported in Medscape; many rare disease patients know the frustration of not having any drugs or treatments available for their disease. 95% of rare disease patients have no…
England’s National Institute for Health and Care Excellence (NICE) recently approved three new thyroid cancer treatments for their National Health Service (NHS). The new treatments provide a wider variety of…
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