Ornithine transcarbamylase (OTC) deficiency is a disorder that can cause comas, seizures, and death, making it necessary for those affected to seek treatment. Arcturus Therapeutics aims to give those with…
UCD Meetup 2019 October 4-5, 2019 Salt Lake City This year's meetup will be a valuable educational event designed to benefit the entire urea cycle disorder (UCD) community. Open to…
Three non-investigational New Drug clinical studies are underway for Urea Cycle Disorders (UCD) and various forms of cirrhosis, initiated by Kaleido Biosciences. Dosing has been initiated in each of these…
According to a story from Pharma Times, four new medications were recently approved for coverage on the Scottish NHS by the Scottish Medicines Consortium (SMC). Some of these drugs are…
The 2019 NUCDF Annual Family Conference This year's conference will be a unique opportunity for researchers, patients, families, and medical experts to come together and spread support and knowledge about…
This year has brought an especially nasty and dangerous strain of the flu. Nobody wants the flu, but contracting the virus while suffering from an underlying condition can be more…
G-M-O. Three letters guaranteed to spark lively, if not heated, debate amongst lifelong friends. These three letters, of course, stand for "genetically modified organisms." Why are they so controversial? Why…
A urea cycle disorder occurs when the body can't break down the ammonia that amino acids produce. Unchecked, ammonia is toxic. According to the National Urea Cycle Disorders Foundation, there…
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