According to a story at medpagetoday.com, a recent study showed that stem cell transplant could be a viable new method for treating scleroderma, and could be more effective than previous…
According to an article from Financial Buzz, the pharmaceutical company CymaBay Therapeutics has announced that the first of its patients have begun to enroll in a long term seladelpar clinical…
RespireRx Pharmaceuticals announced last month it was cleared to resume its ampakine CX717 clinical trials to evaluate the drug’s efficacy in several central nervous system and respiratory disorders, including Pompe…
Shaquem Griffin, an inspiration on and off the field, recently received the Rare Disease Champion Award presented to an outstanding leader in college football and the rare disease community alike,…
Last month, the FDA has granted Achillion Pharmaceuticals orphan drug designation to ACH-4471 for the treatment of patients with C3 Glomerulopathy (C3G). According to the FDA, the Orphan Drug Designation program provides…
New research is helping experts understand the underlying causes of idiopathic pulmonary fibrosis on the molecular scale. When solving any problem, disease included, it is best to start by understanding…
Nothing is worse for a family than hearing the word “cancer,” especially when it involves a child. The Tyson family was ready to start their perfect life eleven years ago.…
New research is being conducted to develop new technologies to detect ovarian cancer. Keep reading or follow the original story here to learn more about the struggles and developments involved…
Madison Simons, a 20-month-old child has visited the hospital more than 12 times and spent more than 50 days at the Baylor Scott & White McLane Children's Hospital this passed…
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