According to EurekAlert!, covering a study conducted by Oregon State University, individuals living with rare diseases are more likely to experience a poorer quality of life. They are at high…
A team of engineers at the University of Connecticut has invented a device which may change medicine as we know it. Researchers say the device could be used as a…
New evidence suggests that home care agencies are not giving Medicare assistance to chronically ill people that legally qualify for it, according to an article from wuwf.org. Take the case…
A new clinical study starts soon and researchers are looking for 75 volunteers. The phase two clinical trial will be testing the safety and tolerability of the drug nilotinib in…
Systemic sclerosis is a chronic and devastating illness. There are no successful treatments, and mortality rates can reach to over 50%. New research by a team at Hospital for Special…
Duke Health just reported that in a recent study, children with cerebral palsy may show improvements from an infusion of their own umbilical cord blood. Recently, a clinical trial including…
Gene therapy is on the rise, and it just might be exactly what many children suffering from genetic disorders need to save their lives. Today reported that an amazing organization…
According to a story from Bioportfolio, trials testing the treatment inclisiran are reaching their enrollment goals ahead of schedule. Inclisiran is currently being tested to reduce LDL-cholesterol in a variety…
Doctors of semi-professional soccer player, Matt Dimbylow, believes he developed Parkinson's disease at the young age of 36-years-old due to a head injury he sustained playing the sport, reports Mirror.…
The Myra and Robert Kraft Family Foundation was established in 2016 creating an initiative to to bring together an alliance between the Harvard Business School with the Broad Institute of…
Tessa Jowell, former Labour party cabinet minister, delivered a moving speech to the UK House of Lords last week. The speech largely concerned her battle with glioblastoma, a rare brain cancer.…
When Kristen Smedley learned her son, Michael, was diagnosed with retinitis pigmentosa, she decided she wouldn't sit back and watch it take away from her son's life, she would take…
It's a fight they didn't choose, but it's a fight they have to face. Individuals diagnosed with sickle cell expressed how much they have to do to get the bare…
According to a story from dailyhealthneeds.com, long term, regular use of protein pump inihibitors (PPI) can majorly increase the risk of contracting stomach cancer. PPIs are commonly used to treat…
The death of a loved one is never easy. It is difficult both to experience and to understand. Mark and Julie Russel lost their son Harry to mitochondrial disease when…
Researchers from Duke Health are hoping to discover new treatments for Lyme disease since the only way to currently manage the disease is by taking consistent antibiotics, which can be…
According to an article from GlobeNewswire, new clinical evidence supports the use of gelpaglutide as a once-weekly treatment for short bowel syndrome. Zealand Pharma completed a Phase I clinical trial…
Rett syndrome might limit 8-year-old Laurel Cooper's ability to speak and do every day tasks, but it doesn't hold back her spunky, sassy attitude, reports University of Wisconsin-Madison News. She will…
15-year-old Jonathan Gutierrez might just be the youngest superhero to date. Recently, a video of him went viral showing how he's sacrificed a lot of his youth to take care…
Originally reported by the Vancouver Sun, children from Langley B.C. are standing up to request access to a potentially life-changing drug as they face the day to day pain onset…
What if we could predict diseases before they happen? What if we could treat diseases like multiple sclerosis and pancreatic cancer before they fully developed. Microsoft is partnering with a…
Physicians at the Canadian Specialist Hospital in Dubai operated on a one-day-old baby with a birth defect called spina bifida, says a recent report. The surgery saved the infant’s life.…
According to an article from FinancialBuzz, the pharmaceutical company Avadel announced that its product FT 218 has been granted orphan drug status by the Food and Drug Administration (FDA) as…
A new fundraising challenge is sweeping all social media platforms once again for amyotrophic lateral sclerosis (ALS), first reported Mom.me. Back in 2014, the ice bucket challenge was a wild success, being…
As an adult living with rare disease, there have been significant gaps in my employment history. I am sure many adults with health complications experience their workforce years this way,…
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