According to a story from Newswise, researchers at the University of Texas Southwestern Medical Center are reporting the a new drug developed for the treatment of rare, pediatric cancers, has…
Researchers at Northwestern University (NU) have published research showing that changes in the brain causing spinocerebellar ataxia type 1 (SCA1) occur at a younger age than previously thought, reports NeuroscienceNews.…
According to a story from the Seattle Times, a massive $150 million gift from Richard and Susan Rogel to the University of Michigan is slated to go towards the school's…
According to a story from mrknewsroom.com, the pharmaceutical companies Merck and AstraZeneca recently announced that the marketing application for the investigational drug olaparib (brand name Lynparza) was recently certified for…
Living with a rare disease provides enough challenges on its own. For residents of Chicago, however, challenges grew even more difficult as pharmacies shut down one after another. Certain areas…
Researchers have developed a new screening test for Pompe disease that is more sensitive than other options, says a report from January. Pompe disease is a muscular disorder caused by…
According to a story from the Independent, father Nick Sireau is worried that Brexit, the United Kingdom's plan to withdraw from the European Union, could affect the ability of his…
An organisation called PatientsLikeMe that helps to represent patients to governments and pharmaceutical companies has published a press release about the results of two recent studies designed to define and…
According to an announcement from the pharmaceutical company Retrophin, Inc., the company is starting to move forward with phase 3 trials for its drug candidate sparsentan. The drug is in…
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