Scientists Discovered the First Effective Alkaptonuria Treatment

In the past, there existed no approved treatments for alkaptonuria (AKU), a rare genetic disorder characterized by homogentisate dioxygenase deficiency. However, according to Medical XPress, this recently changed as British…

Continue Reading Scientists Discovered the First Effective Alkaptonuria Treatment
EMA Gives Positive Opinion on Nitisinone as a Treatment for Alkaptonuria
source: pixabay.com

EMA Gives Positive Opinion on Nitisinone as a Treatment for Alkaptonuria

According to a story from the AKU Society, the European Medicines Agency (EMA) has recently announced a positive opinion on extending the label indication for nitisinone (marketed as Orfadin®). The…

Continue Reading EMA Gives Positive Opinion on Nitisinone as a Treatment for Alkaptonuria
Close Menu