The US FDA has approved the first drug to treat neurotrophic keratitis, a degenerative condition that affects the eyes. Approval of the drug, called Oxervate (cenegermin), is granted to…
Researchers from the University of British Columbia have developed a new genetic model of Parkinson’s disease that is able to model the early changes in synaptic activity associated with the…
Too often we try to interpret the experiences of others without actually communicating with the very individuals we’re trying to better understand. This leads to false impressions and frequently creates…
A team of researchers from the University of North Carolina have been exploring an experimental method of delivering drugs to medulloblastoma that involves converting skin cells into stem cells that…
According to a story from FiercePharma, the US Food and Drug Administration (FDA) has recently ordered a total of 13 different diabetes drugs to begin carrying warning labels about the…
According to a story from Morningstar, Richard Rendina and his family are no strangers to the challenges and tragedy that can come with a cancer diagnosis. Bruce Redina, for example…
According to a story from prnewswire.com, the drug Cablivi, also known as caplacizumab, has been granted marketing authorization by the European Commission. Cablivi is meant to treat acquired thrombotic thrombocytopenic…
Reflection Biotechnologies has announced that the US Food and Drug Administration has awarded Orphan Drug Designation to their RBIO-101 program, which is focused on a gene therapy designed to treat…
Dr Ronny Drapkin, a professor at the University of Pennsylvania says, “One of the things I tell women is that nobody knows your body as well as you do. If…
The rare disease advocacy community is mourning the loss of a wonderful voice, Claire Wineland, who passed away Monday after her battle with Cystic Fibrosis. Claire suffered a stroke on Aug…
There is a new series on Netflix called “Afflicted.” It chronicles the stories of seven people with chronic rare diseases and their struggle to cope with symptoms as they…
Over 55,000 people are diagnosed with pancreatic cancer every year. And about 95 percent of people who are diagnosed with pancreatic cancer will lose their lives from it. Pancreatic…
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