According to a story from Bangor Daily News, Andrea Dole decided to have a home birth for James, her first child. With the support of her partner, Patrick, two midwives,…
The United States Food and Drug Administration has awarded Fast Track Designation to the investigational drug miransertib (ARQ 092), which is being researched as a potential treatment for PIK3CA-related overgrowth…
The process of getting diagnosed with a rare disease, as well as living with one, can be a traumatic experience for patients. Many rare disorders or conditions may commonly cause…
According to a story from pm360online.com, the biopharmaceutical company Insmed Incorporated recently announced that the data from its Phase 3 clinical trial of amikacin liposome inhalation suspension (ALIS). ALIS was…
The first US patient has been dosed with the drug MIN-102 as part of a clinical trial into its effects in patients with adrenomyeloneuropathy. For more information about this, you…
Top-line data from a Phase 3 study of an experimental method of visualising prostate cancer has been announced. While it met the primary endpoint for specificity, it did not meet…
According to a report by The Telegraph, multiple sclerosis patients are being refused an important drug. The drug, known as ocrelizumab will not be funded by The National Institute for…
Recent medical developments have led to new drugs designed to treat rare genetic disorders. However, the high cost of many of these drugs limits the number of patients who have…
The pop-punk singer Avril Lavigne has announced her return to music with a new album that she made while fighting chronic Lyme disease. In a letter to her fans, she…
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