Gene Therapy for Fanconi Anemia Gains IND Clearance From the FDA
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Gene Therapy for Fanconi Anemia Gains IND Clearance From the FDA

According to a story from BioSpace, the gene therapy company Rocket Pharma recently announced that its investigational product candidate RP-L102 recently saw its Investigational New Drug (IND) application gain approval…

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$1.4 Million Donated to Help Bring a Gene Therapy For Tay-Sachs Disease to Clinical Trial
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$1.4 Million Donated to Help Bring a Gene Therapy For Tay-Sachs Disease to Clinical Trial

A $1.4 million dollar donation to the University of Massachusetts Medical School will help to fund research into a gene therapy for Tay-Sachs disease as it transitions from pre-clinical to…

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Proof of Concept Data Highlights Viability of Gene Therapy for Metachromatic Leukodystrophy
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Proof of Concept Data Highlights Viability of Gene Therapy for Metachromatic Leukodystrophy

According to a story from Market Screener, the genetic medicines company Homology Medicines, Inc., recently announced the presentation of data which revealed that the company's proprietary virus vectors, which are…

Continue Reading Proof of Concept Data Highlights Viability of Gene Therapy for Metachromatic Leukodystrophy