According to a story from BioPortfolio, the drug developer Novartis recently announced that the US Food and Drug Administration (FDA) has granted the company's investigational gene therapy AVXS-101, also known…
According to a story from ABC News, the FDA has recently approved Bayer and Loxo Oncology's drug Vitrakvi (larotrectinib) for the treatment of certain forms of solid-tumor cancers (like thyroid…
This is part 2 of Leah's story, click here to read part 1 Leah listened as the doctor explained that her body couldn’t continue to be overexposed in addition to…
According to a story from pm360online.com, the pharmaceutical company Zogenix Inc. recently announced that its experimental drug candidate ZX008, also known as Fintepla®, has performed well in the company's latest…
According to a story from The San Diego Union-Tribune, the Pancreatic Cancer Prevention and Screening Clinic at UC San Diego Moores Cancer center has opened for the first time this…
According to a story from EurekAlert!, the results from a recent Phase 2 clinical trial suggest that a two drug combination could be a useful approach for people with rare,…
Behold the power of sheer will, determination, and tenacity! New York teen Hannea Milliman overcame the rare disorder Parsonage Turner Syndrome - which causes severe pain in the shoulder and arm -…
When Deborah, a New Yorker, flew over to Paris to do an internship for an architecture office, she never knew she would be flying across the world and meeting…
According to a story from BioPortfolio, the gene therapy company Rocket Pharmaceuticals has recently announced that the company's investigational gene therapy RP-L102 has earned both Fast Track and Regenerative Medicine…
According to a story from Reuters, the drug developer BioMarin is looking to make a name for itself in the hemophilia community in a very unique way. The company has…
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