A recently published paper called ‘Biallelic loss of human CTNNA2, encoding αN-catenin, leads to ARP2/3 complex overactivity and disordered cortical neuronal migration’ outlines new research into the genetic basis of…
According to a story from Gloucestershire Live, Emma Robinson, who is only 46 years old, was just told by her doctors that she has terminal cancer. She had vulvar cancer,…
According to 9News, Harry Campbell was born very premature at 27 weeks. Not only this, but his dimensions were almost unfathomable. Harry was able to fit into the palm of…
Gemphire Therapeutics Inc. has been recommended to stop a clinical trial by the Data and Safety Monitoring Board at Emory University School of Medicine. The clinical trial, which ran into…
Let's take a moment during these dog days of summer to recognize the SMA community during SMA awareness month! Spinal muscular atrophy (SMA) is a rare genetic disorder that causes…
The company Epizyme has announced the results of a Phase 2 clinical study of its lead candidate drug, tazemetostat, in the treatment of relapsed or refractory malignant mesothelioma with loss…
A motor neurone disease clinical drug trial will take place in Scotland for the first time in more than twenty years. This study is the first step in a broader…
The top-line results of a pivotal Phase 3 study investigating the drug recorlevTM (levoketoconazole) in patients with endogenous Cushing’s syndrome have been released. The source article, which contains more detailed information,…
An investigational drug called ALT-P7 is being developed as a potential medicine for certain forms of cancer. The drug has received Orphan Drug Designation for the treatment of gastric cancer…
Orkambi, a medication used to treat cystic fibrosis (CF), has improved the lives of some CF patients since approval last year. CF causes thick mucus that leads to difficulty breathing. …
According to a story from Newswise, an organization called the National Comprehensive Cancer Network (NCCN) has recently released treatment guidelines for a rare type of cancer that can affect women…
According to a story from whtc.com, a recent study from the UK is calling into question the widely held belief that fertility treatments could increase the risk of ovarian cancer,…
According to a story from the University of Toledo, a team of researchers from the school have successfully designed a molecule affectionately dubbed "Sweet-P" that can stop the movement of…
According to a story from SFGate, many survivors of childhood cancers are plagued with financial burdens for the rest of their lives. This is because treatment of childhood cancer can…
The US FDA has awarded Orphan Drug status to the investigational drug NSI-189 for use by people with Angelman syndrome. You can read the source article here, at Nasdaq. About…
According to a story from The Guardian, a recent study suggests that cannabidiol, or CBD, could magnify the effectiveness of treatment for pancreatic cancer. CBD is naturally found in the…
The US Food and Drug Administration (FDA) has awarded Orphan Drug Designation to the experimental drug ALN-TTRsc02. Alnylam Pharmaceuticals Inc. is developing ALN-TTRsc02 as a possible treatment for transthyretin-mediated amyloidosis.…
According to MedPage Today, a phase III study showed that 6 additional months of chemotherapy for maintenance led to a sizable increase in the 5-year overall survival rate for…
According to News Medical, a team of researchers from London have created new technologies that may aid in further understanding Duchenne muscular dystrophy (DMD). Not only this, but the new…
According to BioSpace, a new treatment for pemphigus vulgaris (PV) has been recently approved by the U.S. Food and Drug Administration. The treatment, Rituxan (rituximab), is geared towards adults who have…
The European Medicines Agency has awarded Orphan Drug designation to selumetinib for the treatment of neurofibromatosis type 1. You can read the source press release here, on Merck’s website. About…
According to a story from Hospital Healthcare Europe, The European Medicines Agency approved Kineret last year, an anti-inflammatory drug developed by Sobi. In the UK, Kineret is an approved treatment…
According to a story from Kaiser Health News, many patients that are dealing with chronic pain feel stuck in the debate over opioids in the US. As the ongoing crisis…
According to a story from World Lifestyle, Emmy and Jake were high school sweethearts, destined for love. Indeed, even after years apart, the two found themselves together again after graduating…
According to a story reported by Global News Canada, Michelle Quinlan said it was seven years before doctors correctly diagnosed her daughter, Avery, with Coffin-Siris syndrome. A new project by…
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