There’s good news coming out of MIT this week. In an article on Medical Xpress, new findings are coming out using CRISPR, a tool that is known for its ability…
Filipa Vance, a woman who was diagnosed with osteosarcoma when she was 15, now celebrates 30 years of living post-diagnosis. Filipa is now cancer-free, but lives with many of the…
The US Food and Drug Administration has awarded Orphan Drug Designation to the drug lenabasum as a treatment for dermatomyositis. The use of lenabasum for treating this condition, and others,…
Pets brighten the lives of many people across the world. There are a variety of studies and pieces of evidence that point to pets improving the quality of life for…
According to a story from Medical Xpress, a long term study testing a treatment for autosomal dominant polycystic kidney disease (ADPKD) has recently concluded. The treatment in question is a…
Patients living with PKU (phenylketonuria) have hope as researchers look into new drugs that may help the body break down phenylalanine. PKU is an genetic disease in which the body lacks…
I am a patient who has ITP and attended the PDSA conference this year in Cleveland, Ohio. I learned so many new things from other attendees and from the outstanding…
As vice chair of the National Comprehensive Cancer Network ‘s (NCCN) committee on multiple myeloma, Dr. Natalie Callander helps to set guidelines for effective evaluation and treatment. The NCCN commonly…
The organisations Takeda Pharmaceutical Company and Ovid Therapeutics are collaborating over the development of the experimental drug TAK-935/OV935 as a possible treatment for several rare epilepsy syndromes. Takeda has just…
Aidan Maddocks, 14, from Pietermaritzburg, was diagnosed with Biliary Atresia at birth, a childhood liver disease that only affects 1 in 10,000–15,000 live births. He was given a life expectancy…
Results from a Phase 2 clinical trial comparing the effects of baricitinib to a placebo in patients with systemic lupus erythematosus (SLE) have been announced. For more detailed information, please…
Researchers from the Newcastle University are investigating the personal and financial impacts of persistent facial pain on patients in the UK, and what can be done to improve medical…
According to a story from ABC News, Alexia Baier was four years old when she came down with strep throat, an infection caused by group A streptococcus bacteria. It is a…
According to a story from the Los Angeles Daily News, for children with debilitating rare illnesses like cerebral palsy, epilepsy, or muscular dystrophy, it can often take a long time…
The National Center for Complementary and Integrative Health (NCCIH) has launched an app that is designed to inform people about the science behind herbs and herbal supplements commonly marketed for…
According to a story from nature.com, gene therapy administered to fetuses could help curtail some of the worst effects of deadly genetic disorders. In a mouse model study, fetal delivery…
A married couple from Grimsby in England are planning to undergo kidney transplant surgery. Paula will donate her kidney to her husband Kevin, who has polycystic kidney disease. The original…
According to a story from pm360online.com, the company PledPharma recently announced that its drug candidate Aladote has completed its first safety evaluation with a positive result. Aladote is in development…
According to a story from healthline.com, many cancer survivors that have been treated with chemotherapy wind up facing significant challenges after their treatment. One such example is a phenomenon known…
Novartis has teamed up with Numinous Games to develop Galaxies of Hope, an app that is designed to support the neuroendocrine tumour (NET) community. You can read the original source…
Having a child was an exciting moment for the Blackwood family. Their son, Sam, is now nine years old. It was around his first birthday, however, that they started to…
Jaiden, a twelve-year-old boy, has been diagnosed with stiff skin syndrome, a rare disease that causes his skin to harden. His family has been sharing their experiences with the condition.…
I'll start this article, like many others, by mentioning that although I'm convinced I know everything about everything because I minored in biology in college, I'm really not a doctor.…
According to a story from Fierce Biotech, recent research is highlighting the possibility that PARP inhibitors, a type of targeted therapy that it mostly used to treat breast cancer and…
According to Medical Xpress, Professor and Doctor Joseph Wu is looking into the complications of DNA testing and genetic mutations. Specifically, the confusion of gene mutations that are labeled "variants…
© Copyright 2024 Patient Worthy
Sign Up With a Patient Worthy Account and Share Your Rare Story
- OR -
Make a difference, share your experiences and get paid. Opt-in and join Patient Worthy's panel for paid opportunities such as surveys, market research, patient advisory panels and more.
- OR -
Make a difference, share your experiences and get paid. Opt-in and join Patient Worthy's panel for paid opportunities such as surveys, market research, patient advisory panels and more.
