Could This Gene Therapy be a Breakthrough Treatment for Tay-Sachs Disease?

According to a story from the Times of Israel, a team of researchers associated with the University of Massachusetts appear to have discovered a potential breakthrough in regards to the…

Continue Reading Could This Gene Therapy be a Breakthrough Treatment for Tay-Sachs Disease?
First Ever International Burden of Illness Survey for Rett Syndrome to be Conducted
TeroVesalainen / Pixabay

First Ever International Burden of Illness Survey for Rett Syndrome to be Conducted

According to a story from BioSpace, the biopharmaceutical company Newron Pharmaceuticals S.p.A. has announced that is partnering with the Rett syndrome disease community in order to sponsor an all new…

Continue Reading First Ever International Burden of Illness Survey for Rett Syndrome to be Conducted

The AI Revolution in Rare Disease Drug Discovery

A recent announcement by Atomico, one of Europe’s largest venture capital firms based in London, introduced its new partner Healx. The startup can boast of having the world’s most comprehensive…

Continue Reading The AI Revolution in Rare Disease Drug Discovery
Marketing Applications for a Possible Neuromyelitis Optica Spectrum Disorder Drug Have Been Accepted in the US and EU
LhcCoutinho / Pixabay

Marketing Applications for a Possible Neuromyelitis Optica Spectrum Disorder Drug Have Been Accepted in the US and EU

According to a story from BioSpace, Chugai Pharmaceutical Co., Ltd. has recently announced that the Marketing Authorisation Application for the its drug satralizumab has been accepted by the European Medicines…

Continue Reading Marketing Applications for a Possible Neuromyelitis Optica Spectrum Disorder Drug Have Been Accepted in the US and EU
Close Menu