When Zika virus appeared in the news in 2015 and 2016, one of the biggest warnings was for pregnant women: be careful, as this can cause birth defects. Most…
According to a story from BioSpace, the biotechnology company Tyme, Inc. has just announced that it has earned Orphan Drug designation for its experimental product candidate SM-88. SM-88, also known…
According to a story from Parkinson's News Today, a recent study may have discovered the origins of chronic pain and damage to the sensory nerves as found in some cases…
A recent article in The American Journal of Managed Care (AJMC) heralds the approval of a third CAR T-cell therapy, called Tecartus. Kite Pharma’s cell-based gene therapy is the first…
As reported in Parkinson's News Today; Daniel Vesely had a hunch. He had been using mannitol, an easy to access over-the-counter sweetener and supplement often used by people with diabetes,…
Metformin is a popular drug used by type 2 diabetes patients. According to recent interviews conducted by reporters for Medical Xpress, a team of researchers conducted parallel rodent and…
People with genetic diseases or disorders may experience differences on a physiological level. For example, shares Medical XPress, fragile X syndrome (FXS) results in less primary cilia. Since primary cilia…
August is recognized as Spinal Muscular Atrophy Awareness Month. The goal of this event is to help spread information about this rare disorder among the general public and the broader…
According to a story from the CureDuchenne Blog, Dr. Kevin Flanigan of Nationwide Children's Hospital has recently dosed two Duchenne muscular dystrophy patients with an experimental gene therapy. This gene…
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