In a news release from June 29, 2021, biotechnology company Neurogene Inc. shared that its adeno-associated virus (AAV) encoding a codon-optimized human CLN5 transgene (hCLN5) received Orphan Drug designation from…
According to the Centers for Disease Control, one in ten people are carriers of a disease-causing bacteria called Neisseria meningitidis. In most cases, they will not experience adverse effects. However,…
An exciting article in the Guardian published last year and a confirming article published this month state that new diagnostic technology has shown ‘impressive results’. This test can spot tumors…
People are rushing to get in shape for summer; it's common to see the gyms a little more full than normal. While exercise is good for you, it's important not…
An Orphan Drug designation is granted to drugs or biologics intended to treat patients with rare diseases or conditions, affecting less than 200,000 Americans. Because it can sometimes be difficult…
In the past, antipsychotics were recommended as a potential treatment for patients with Parkinson's disease (PD). This is because, in later stages of PD, patients may experience Parkinson's psychosis, which…
Patient Worthy was a media partner at this year's NORD Living Rare, Living Stronger Patient and Family Forum. This is an annual event hosted by the National Organization for Rare…
From June 4-8, 2021, the American Society of Clinical Oncology (ASCO) held its Annual Meeting to discuss trends and research within the oncology field. According to Cancer Therapy Advisor,…
As seen in a press release by Bioindustry; the UK BioIndustry Association (BIA) has published findings from a survey on the public’s interest in supporting rare access to affordable medicine…
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