Study Data Shows Promise in LYS-SAF302 for Sanfilippo Syndrome Type A

Both the 3rd Annual Gene Therapy for Neurological Disorders meeting and the ADVANCE 2022 Sanfilippo Community Conference were held in July 2022. During both meetings, researchers presented new data from…

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Rare Classroom: Alkaptonuria
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Rare Classroom: Alkaptonuria

Welcome to the Rare Classroom, a new series from Patient Worthy. Rare Classroom is designed for the curious reader who wants to get informed on some of the rarest, most…

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