Roivant and Priovant Secure FDA Approval for First Targeted Oral Therapy for Dermatomyositis

As reported on Pharma Phorum, Roivant Sciences and its subsidiary Priovant Therapeutics have received U.S. Food and Drug Administration (FDA) approval for Lisraya (brepocitinib), marking the first targeted treatment specifically…

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AstraZeneca Secures Global Rights to EGFR-Targeted Lung Cancer Therapy ZEGFROVY

As reported on Business Wire, AstraZeneca has finalized its previously announced licensing agreement with Dizal Pharmaceutical, gaining exclusive worldwide rights to develop and market ZEGFROVY (sunvozertinib), an oral, irreversible epidermal…

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Basking Biosciences formulates Reversable Clot Busting Therapy for Acute Stroke

Treating acute ischemic strokes involves a precarious clinical balance: physicians must dissolve arterial clots to save brain tissue without triggering catastrophic intracranial hemorrhaging. To address the severe bleeding risks associated…

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Lorelei, the SYNGAP1 Warrior

Editor's Note: Patient Worthy is honored to share the following article, originally published by our friends at CURE SYNGAP1. To see the article in its original format, please click here.…

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Orsini Selected as Specialty Pharmacy Partner for Newly Approved Dermatomyositis Therapy LISRAYA

As reported on PR NewsWire, Orsini has been named a specialty pharmacy partner for Priovant’s LISRAYA™ (brepocitinib), a once-daily oral treatment recently approved by the US Food and Drug Administration…

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CARDIO-TTRansform: Eplontersen Fails to Improve Cardiovascular Outcomes When Added to Standard Therapy in ATTR-CM

As reported on Healio, the phase 3 CARDIO-TTRansform study, the largest clinical trial conducted to date in patients with transthyretin amyloidosis with cardiomyopathy (ATTR-CM), found that adding eplontersen to contemporary…

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FDA Announces Nationwide Recall of Certain Thyroid Medication Due to Excess Potency Risk

As reported on The Hill, Vitruvias Therapeutics has initiated a voluntary nationwide recall of a specific lot of thyroid medication after testing indicated the tablets may contain higher-than-labeled potency, according…

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Vera’s Trutakna Shows Signs of Preserving Kidney Function in IgA Nephropathy, Challenging Voyxact’s Differentiation

As reported on BioSpace, Vera Therapeutics’ newly approved IgA nephropathy (IgAN) treatment, Trutakna, is showing early evidence that it may help preserve kidney function, a benefit that had recently drawn…

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New Consensus Recommendations Aim to Strengthen Communication and Decision-Making in Neuroblastoma Care

As reported on GlobeNewswire, a newly published set of expert consensus recommendations is seeking to improve the care experience for children diagnosed with neuroblastoma and the families who support them.…

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Investigational Therapy Shows Promise for Guillain-Barré Syndrome in Late-Stage Testing

As reported on Newsweek, a novel experimental treatment for Guillain-Barré syndrome (GBS) may represent a major advance for patients living with the rare neurological disorder. New findings released by biotechnology…

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FDA Authorizes Lantheus’ Tau PET Imaging Agent for Alzheimer’s Disease Evaluation

As reported on Fierce BioTech, the U.S. Food and Drug Administration has granted approval to Lantheus’ positron emission tomography (PET) imaging agent Tauklarify (MK-6240), expanding diagnostic options for the assessment…

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FDA Approves Regeneron’s Pasatru for Fibrodysplasia Ossificans Progressiva, Expanding Treatment Options

As reported on BioSpace, the U.S. Food and Drug Administration has approved Regeneron’s Pasatru (garetosmab) for adults with fibrodysplasia ossificans progressiva (FOP), a rare genetic disorder that causes bone to…

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TransThera Secures China’s First Approval for Patients With FGFR Inhibitor-Resistant Cholangiocarcinoma

As reported by allsci, China’s National Medical Products Administration (NMPA) has granted conditional approval to TransThera Sciences’ Yochanra (tinengotinib) for adults with unresectable, advanced, or metastatic cholangiocarcinoma (CCA) carrying FGFR2…

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Zydus Introduces India’s First Once-Daily Nebulized LAMA for COPD Maintenance

As reported by PharmaBiz, Zydus Lifesciences has announced the launch of Revahale (revefenacin), a once-daily nebulized long-acting muscarinic antagonist (LAMA) for the maintenance treatment of chronic obstructive pulmonary disease (COPD).…

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AstraZeneca Ends Phase 3 Volrustomig Study in Lung Cancer After Interim Review Signals Low Likelihood of Success

As reported on BioSpace, AstraZeneca has discontinued a pivotal Phase 3 trial evaluating its investigational bispecific antibody volrustomig in advanced non-small cell lung cancer (NSCLC) after an interim analysis indicated…

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Tirzepatide May Enhance Biologic Therapy Outcomes in Psoriatic Arthritis Patients With Obesity

New observational research suggests that addressing obesity alongside inflammatory joint disease could improve treatment outcomes for people with psoriatic arthritis (PsA). As reported on MedIndia, a recent propensity score-matched analysis…

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Impending PPAR-Targeted Therapies Expand Treatment Possibilities for Primary Biliary Cholangitis

As reported on News Medical, researchers are highlighting a new class of therapies that could improve outcomes for people living with primary biliary cholangitis (PBC), a chronic autoimmune liver disease…

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LEVI-04 Shows Promise as a Novel Non-Opioid Therapy for Knee Osteoarthritis in Phase 2 Trial

A recent study shared by The Lancet shows that a first-in-class investigational therapy targeting neurotrophin-3 (NT-3) significantly reduced pain and improved function in patients with knee osteoarthritis (OA), according to…

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