NDA for Potential Progressive Familial Intrahepatic Cholestasis Treatment Cleared by FDA
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NDA for Potential Progressive Familial Intrahepatic Cholestasis Treatment Cleared by FDA

According to a press release from the rare liver disease company Albireo Pharma, Inc., the US Food and Drug Administration (FDA) has accepted its New Drug Application (NDA) for odevixibat.…

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Initiation of Global Phase 3 Trial of Alagille Syndrome Treatment
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Initiation of Global Phase 3 Trial of Alagille Syndrome Treatment

Albireo has recently initiated their Phase 3 ASSERT trial, according to GlobeNewswire. This study will evaluate odevixibat as a treatment for Alagille syndrome. This therapy fits well with Albireo's mission,…

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Odevixibat Shows Promise in Progressive Familial Intrahepatic Cholestasis
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Odevixibat Shows Promise in Progressive Familial Intrahepatic Cholestasis

According to a story from GlobeNewswire, the rare disease liver company Albireo Pharma, Inc., recently announced positive results from a phase 3 study testing the company's experimental drug odevixibat as…

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New 5-Year Survival Data Available on Maralixibat for PFIC2

This year, the Digital International Liver Congress took place online from August 27-29, thanks to COVID-19. During the conference, biopharmaceutical company Mirum Pharmaceuticals announced data from its Phase 2 INDIGO…

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Phase 3 Trial of Experimental Progressive Familial Intrahepatic Cholestasis Drug for Pediatric Patients Begins
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Phase 3 Trial of Experimental Progressive Familial Intrahepatic Cholestasis Drug for Pediatric Patients Begins

According to a story from drugs.com, the biopharmaceutical company Mirum Pharmaceuticals recently announced that they have begun dosing the first patient in a phase 3 clinical trial. This clinical trial…

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4-Year-Old Girl Joins Clinical Trial to Relieve Itching Associated With Alagille Syndrome
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4-Year-Old Girl Joins Clinical Trial to Relieve Itching Associated With Alagille Syndrome

According to a story from abc13.com, Makenna Brown, a four-year-old girl from Texas, has been plagued by relentless itching thanks to her Alagille syndrome, a rare genetic disorder. Her distressed…

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Experimental Treatment for Biliary Atresia Gets Orphan Drug Designation in the EU
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Experimental Treatment for Biliary Atresia Gets Orphan Drug Designation in the EU

According to a story from Market Screener, the drug developer Albireo Pharma, Inc., recently announced that its investigational product candidate A4250 has earned Orphan Drug designation from the European Commission.…

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New Development Deal Struck for Experimental Alagille Syndrome Treatment
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New Development Deal Struck for Experimental Alagille Syndrome Treatment

According to a story from prnewswire.com, the drug developer Mirum Pharmaceuticals recently announced that is has entered an agreement with Shire which grants exclusive rights for marketing and development of…

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By Observing the Effects of Alagille Syndrome, Researchers Discover How Liver Tissue Can Transform and Heal
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By Observing the Effects of Alagille Syndrome, Researchers Discover How Liver Tissue Can Transform and Heal

According to a story from PR Newswire, a group of scientists have managed to discover a mechanism that allows the liver to repair damage it has sustained. This discovery may…

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