First International Awareness Day for Alagille Syndrome was Held January 24th
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First International Awareness Day for Alagille Syndrome was Held January 24th

International Alagille Awareness Day The very first International Alagille Awareness day was held on January 24th, 2020. What is Alagille syndrome? It is a rare disease which effects the heart,…

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Phase 3 Trial of Experimental Progressive Familial Intrahepatic Cholestasis Drug for Pediatric Patients Begins

According to a story from drugs.com, the biopharmaceutical company Mirum Pharmaceuticals recently announced that they have begun dosing the first patient in a phase 3 clinical trial. This clinical trial…

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4-Year-Old Girl Joins Clinical Trial to Relieve Itching Associated With Alagille Syndrome
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4-Year-Old Girl Joins Clinical Trial to Relieve Itching Associated With Alagille Syndrome

According to a story from abc13.com, Makenna Brown, a four-year-old girl from Texas, has been plagued by relentless itching thanks to her Alagille syndrome, a rare genetic disorder. Her distressed…

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Experimental Treatment for Biliary Atresia Gets Orphan Drug Designation in the EU
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Experimental Treatment for Biliary Atresia Gets Orphan Drug Designation in the EU

According to a story from Market Screener, the drug developer Albireo Pharma, Inc., recently announced that its investigational product candidate A4250 has earned Orphan Drug designation from the European Commission.…

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New Development Deal Struck for Experimental Alagille Syndrome Treatment
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New Development Deal Struck for Experimental Alagille Syndrome Treatment

According to a story from prnewswire.com, the drug developer Mirum Pharmaceuticals recently announced that is has entered an agreement with Shire which grants exclusive rights for marketing and development of…

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PatientWorthy is Offering Two Tickets to the First Annual Alagille Syndrome Alliance Gala
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PatientWorthy is Offering Two Tickets to the First Annual Alagille Syndrome Alliance Gala

PatientWorthy will be offering a pair of tickets to the Alagille Syndrome Alliance's (ALGSA) First Annual Gala. The tickets will be available for patients or caregivers in the San Diego…

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By Observing the Effects of Alagille Syndrome, Researchers Discover How Liver Tissue Can Transform and Heal
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By Observing the Effects of Alagille Syndrome, Researchers Discover How Liver Tissue Can Transform and Heal

According to a story from PR Newswire, a group of scientists have managed to discover a mechanism that allows the liver to repair damage it has sustained. This discovery may…

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