Gene Therapy Could Cure Irreversible Blindness for X-Linked Retinitis Pigmentosa
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Gene Therapy Could Cure Irreversible Blindness for X-Linked Retinitis Pigmentosa

As reported in Biospace, a new gene therapy has made notable progress towards curing x-linked retinitis pigmentosa, a disease responsible for sight loss in men. Until now, the disease irreversibly…

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One London Teenager Raises Enough Money for the First Clinical Trial for Choroideremia
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One London Teenager Raises Enough Money for the First Clinical Trial for Choroideremia

  Tommy Salisbury is eighteen years old. Unlike many teenagers, he is making big moves in the fundraising community and working hard to be a leader in efforts to find…

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Choroideremia Can Lead to Blindness – But Gene Therapy Might Be Able to Halt It
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Choroideremia Can Lead to Blindness – But Gene Therapy Might Be Able to Halt It

An article recently published by the Guardian shared the stories of three families affected by recent breakthroughs in gene therapy treatments. What is Gene Therapy? Gene therapy is an increasingly…

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New Mutations Identified in Study of Five Polish Families With Choroideremia

According to a scientific study published in the Orphanet Journal of Rare Diseases, a team of researchers were able to identify the mutations responsible for choroideremia in five families of Polish descent.…

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Experimental Treatment for Choroideremia Earns RMAT Designation
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Experimental Treatment for Choroideremia Earns RMAT Designation

According to a story from BioPortfolio, the gene therapy company Nightstar Therapeutics recently released an announcement that the FDA issued Regenerative Medicine Advanced Therapy (RMAT) designation for its investigational product…

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High-School Science Project Identifies Mutant Choroideremia Gene
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High-School Science Project Identifies Mutant Choroideremia Gene

Exploding paper-mache volcanoes. Solar systems made of styrofoam balls. Carrot electricity. I remember the sights, smells, and sounds of my high school science fair as it was yesterday. Those earth-shattering…

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This Boy with Choroideremia is Changing the Lives of Baseball Players Left and Right
Source: Pixabay

This Boy with Choroideremia is Changing the Lives of Baseball Players Left and Right

Choroideremia is a disorder that progressively causes you to lose your sight. There is no cure. According to Pinstriped Prospects earlier this year, Markie DeVoe is a 12-year-old living with the…

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