In early November, global biotechnology company BioMarin Pharmaceutical Inc. ("BioMarin") announced the acceptance of its New Drug Application (NDA) for vosoritide. The investigational injectable treatment is designed to treat pediatric…
BioMarin Pharmaceutical Inc. has recently submitted a new drug application (NDA) for their achondroplasia treatment, vosoritide. This once a day injection is for children who live with the disorder, and…
Ascendis Pharma has just announced that their investigative therapy for achondroplasia called TransCon CNP has just received Orphan Drug Designation from the European Commission. This same designation has already been…
As originally reported in Live 99.9; when Melissa and Chris Courson found out the baby they were expecting in a few months would be born with the rare thantophoric dysplasia,…
As reported in RadioFreeEurope, Russian biologist Denis Rebrikov is currently challenging the norm of caution regarding gene-editing in the science world, with efforts to gain the go-ahead from Russia to…
According to a story from BBC, nine year old Sam Short has been trying an experimental drug for three years that aims to improve his growth. This is because he…
According to a story from abc13.com, Washington state appears to be poised to become the third US state to ban dwarf tossing, a humiliating public spectacle used as entertainment in…
Sam Nicholson was a small child. His mother, Erica, did not find this surprising. Erica is only about five feet tall. She weighs about 100 pounds. She describes all of…
A 64 year old woman recently passed away on May 11, 2018. Ellen Maud Bennett had been feeling unwell for years, and when seeking out medical treatment, her doctors did…
According to a story from IRB Barcelona, a recent conference has brought together researchers from around the world that are dedicated to the study of the cell cycle and two…
Mallory and Dave Holmes were excited. Like many couples, they were eagerly awaiting the birth of their first child. After 20 weeks of pregnancy, however, the couple received news that…
3D printing has officially hit the medical field and it's already making noise, reports The Jerusalem Post. Recently, 3D printing was used in Israel for orthopedic surgery and found great success.…
Ellie Simmonds is a dominate Paralympic swimmer having won five times in her 23-years and was honored locally for her success, reported Border Telegraph. Just recently, she attended to a…
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