Glycogen Storage Disease Type I Archives

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Life as a Parent of a Child With Glycogen Storage Disease: A Rare Disease Story From the Czech Republic

James Moore
November 20, 2019
Glycogen Storage Disease Type I
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When your child is constantly at risk of hypoglycemia and their health and life is threatened in the case of any major problem, you have no other choice but to…

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The First Patient Has Been Dosed on a Clinical Trial of an Investigational Gene Therapy for the Treatment of GSDIa

Anna Hewitt
August 6, 2018
Glycogen Storage Disease Type I
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According to a source article that can be found here on Ultragenyx’s website, the first patient has been dosed in a trial of an investigational gene therapy called DTX401 that…

Life as a Parent of a Child With Glycogen Storage Disease: A Rare Disease Story From the Czech Republic

The First Patient Has Been Dosed on a Clinical Trial of an Investigational Gene Therapy for the Treatment of GSDIa

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