Zachary Thomas Newborn Screening Act Could Introduce MPS I to Alabama’s Newborn Screening Panel
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Zachary Thomas Newborn Screening Act Could Introduce MPS I to Alabama’s Newborn Screening Panel

Zachary Thomas has been an advocate for the mucopolysaccharidosis type I (MPS I) community since he was born.  Newborn screening is a public health initiative that tests newborn babies for…

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FDA Grants Rare Pediatric Disease Designation to AVR-RD-05 for Hunter Syndrome
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FDA Grants Rare Pediatric Disease Designation to AVR-RD-05 for Hunter Syndrome

According to an article published in Yahoo, the FDA has recently granted the Rare Pediatric Disease designation to AVR-RD-05, a gene therapy for Hunter syndrome. This designation is reserved for…

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