Sanofi is Making Strides in Lysosomal Storage Disease Research

Sanofi There are an estimated 350 million rare disease patients across the world. Many conditions still don't have treatments. However, there are scientists dedicating their lives solely to this endeavor.…

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Program Aims to Help Diagnose Certain Rare Diseases More Quickly
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Program Aims to Help Diagnose Certain Rare Diseases More Quickly

According to a story from PR Newswire, a new program called The Lantern Project is working to provide a free testing program that allow doctors to more quickly diagnose patients…

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The First Patient Has Been Treated in a Gene Therapy Study for MPS I
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The First Patient Has Been Treated in a Gene Therapy Study for MPS I

The first patient has been treated in the Empowers study, a clinical trial investigating an experimental gene editing therapy for the treatment of mucopolysaccharidosis type I. The source article, which…

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