FDA Accepts Priority Review NDA for Potential Niemann-Pick Disease Type C Drug
source: pixabay.com

FDA Accepts Priority Review NDA for Potential Niemann-Pick Disease Type C Drug

According to a story from globenewswire.com, the US Food and Drug Administration (FDA) recently accepted the New Drug Application (NDA) for arimoclomol. This application is for the use of the…

Continue Reading FDA Accepts Priority Review NDA for Potential Niemann-Pick Disease Type C Drug
New Drug Application for Niemann-Pick Disease Type C Treatment
source: pixabay.com

New Drug Application for Niemann-Pick Disease Type C Treatment

Orphazyme has recently submitted their New Drug Application to the FDA for their Niemann-Pick disease type C (NPC) treatment, arimoclomol. This application comes after the biopharmaceutical company was already granted…

Continue Reading New Drug Application for Niemann-Pick Disease Type C Treatment
New Drug Application for Niemann-Pick Disease Type C Treatment Submitted Under Rolling Review
source: pixabay.com

New Drug Application for Niemann-Pick Disease Type C Treatment Submitted Under Rolling Review

According to a story from globenewswire.com, the biopharmaceutical company Orphazyme A/S has recently announced that it has submitted its New Drug Application (NDA) for its experimental treatment arimoclomol to the…

Continue Reading New Drug Application for Niemann-Pick Disease Type C Treatment Submitted Under Rolling Review
Family Affected by Niemann-Pick Disease Type C Faces Challenges During COVID-19
source: pixabay.com

Family Affected by Niemann-Pick Disease Type C Faces Challenges During COVID-19

According to a story from Spectrum News, the Andrews family has been dealing with a rare disease called Niemann-Pick disease type C for years. Parents Pam and Chris knew early…

Continue Reading Family Affected by Niemann-Pick Disease Type C Faces Challenges During COVID-19
Study: Arimoclomol Shows Positive Results in the Treatment of Niemann-Pick Disease
source: pixabay.com

Study: Arimoclomol Shows Positive Results in the Treatment of Niemann-Pick Disease

  Orphazyme, a biopharmaceutical company, has recently released the data from their study of arimoclomol. This product is meant for the treatment of Niemann-Pick disease type C (NPC). Orphazyme specializes…

Continue Reading Study: Arimoclomol Shows Positive Results in the Treatment of Niemann-Pick Disease

Phase 1 Trial for Niemann-Pick Disease Type C Has Completed Enrollment

Niemann-Pick disease type C (NPC) is a rare disease caused by a defected NPC protein. In a healthy individual, this protein helps the body process cholesterol. Those diagnosed with NPC experience…

Continue Reading Phase 1 Trial for Niemann-Pick Disease Type C Has Completed Enrollment
This Company Just Provided a Grant for a Niemann-Pick Disease Type C Screening Program
Pexels / Pixabay

This Company Just Provided a Grant for a Niemann-Pick Disease Type C Screening Program

According to a story from ir.stockpr.com, the biotechnology company Cyclo Therapeutics, Inc. (previously known as CTD Holdings) has recently thrown its support behind a Niemann-Pick Disease Type C newborn screening…

Continue Reading This Company Just Provided a Grant for a Niemann-Pick Disease Type C Screening Program
ICYMI: FDA Approves Expanded Access Application of Experimental Niemann-Pick Type C Drug
rawpixel / Pixabay

ICYMI: FDA Approves Expanded Access Application of Experimental Niemann-Pick Type C Drug

According to a press release from CTD Holdings, the American Food and Drug Administration (FDA) recently approved an Expanded Access application from a physician to treat a pediatric Niemann-Pick disease…

Continue Reading ICYMI: FDA Approves Expanded Access Application of Experimental Niemann-Pick Type C Drug
FDA Approves a Program for Expanded Treatment Access in Niemann-Pick Disease Type C
rawpixel / Pixabay

FDA Approves a Program for Expanded Treatment Access in Niemann-Pick Disease Type C

According to a story from ir.stockpr.com, the biotechnology company CTD Holdings, Inc., recently announced that the US Food and Drug Administration (FDA) has issued an approval for an individual Investigational…

Continue Reading FDA Approves a Program for Expanded Treatment Access in Niemann-Pick Disease Type C

CTD Holdings Gives Presentation on Investigatory Niemann-Pick Type C Drug at Family Support and Medical Conference

According to a press release from CTD Holdings, a biotechnology company based in Gainesville, Florida, the Company recently presented data collected from their investigatory Niemann-Pick Disease treatment, Trappsol Cyclo, to…

Continue Reading CTD Holdings Gives Presentation on Investigatory Niemann-Pick Type C Drug at Family Support and Medical Conference
Close Menu