Singapore: 29,000 Donors Responded to a Plea By Devdan’s Parents For a One Time Gene Therapy Treatment That Costs $2.8 Million
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Singapore: 29,000 Donors Responded to a Plea By Devdan’s Parents For a One Time Gene Therapy Treatment That Costs $2.8 Million

According to YAHOO News, twenty-two-month-old Devdan has a rare disease called type 2 spinal muscular atrophy (SMA2) which affects nerve cells that control muscles. If left untreated progressive muscle weakness…

Continue Reading Singapore: 29,000 Donors Responded to a Plea By Devdan’s Parents For a One Time Gene Therapy Treatment That Costs $2.8 Million
Evrysdi (risdiplam) Shows Promising Results in Tiniest Spinal Muscular Atrophy Patients
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Evrysdi (risdiplam) Shows Promising Results in Tiniest Spinal Muscular Atrophy Patients

by Lauren Taylor from In The Cloud Copy Spinal muscular atrophy or SMA is a disease that affects the patient’s central nervous system, peripheral nervous system, and skeletal muscles or…

Continue Reading Evrysdi (risdiplam) Shows Promising Results in Tiniest Spinal Muscular Atrophy Patients
This Organization is Offering Spinal Muscular Atrophy Patients Financial Aid for Treatment
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This Organization is Offering Spinal Muscular Atrophy Patients Financial Aid for Treatment

According to a story from SMA News Today, the Patient Access Network (PAN) Foundation announced that it is now offering financial assistance to help patients living with the rare disease…

Continue Reading This Organization is Offering Spinal Muscular Atrophy Patients Financial Aid for Treatment