On July 8, 2021, gene therapy company Lysogene shared that its gene therapy candidate LYS-GM101, for patients with GM1 gangliosidosis, received Fast Track designation from the FDA. Currently, no treatments…
The GM1 Family Meeting September 20th, 2019 San Diego, CA This GM1 Family Meeting is intended for all GM1 patients and their families. Don't miss this opportunity to learn about…
Cure GM1 Foundation is hosting a family meeting filled with hope on Friday, September 20th! This gathering will be focused on community, clinical development and research updates, patient advocacy, and…
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