medical research – Page 11

Photo courtesy of Dr. Seth Lederman

How Tonix is Working to Change the Prader-Willi Syndrome (PWS) Treatment Landscape: A Discussion with Dr. Seth Lederman

Post author:Jessica Lynn
Post published:February 23, 2023
Post category:Prader-Willi Syndrome

Dr. Seth Lederman founded Tonix Pharmaceuticals with a deep desire to change the treatment landscape for patients. The company’s rich pipeline features therapeutic options for fibromyalgia, post-traumatic stress disorder (PTSD),…

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Early-Stage Ovarian Cancer Characterized by Microbe Colonization

Post author:Jessica Lynn
Post published:February 21, 2023
Post category:Ovarian Cancer

Early identification and diagnosis of cancers or rare conditions can significantly improve patient outcomes. For example, early ovarian cancer detection contributes to a better prognosis. Yet many women remain…

source: pixabay.com

New Genetic Test Could Aid Ovarian Cancer Care

Post author:Jessica Lynn
Post published:February 21, 2023
Post category:Ovarian Cancer

Scientists are always looking into new ways to advance treatments and improve patient outcomes, especially in disease states with high mortality rates. Currently, ovarian cancer is associated with a…

Five-Year Survival Rate Rises for Pancreatic Cancer

Post author:Jessica Lynn
Post published:February 16, 2023
Post category:Pancreatic Cancer

Pancreatic cancer unfortunately comes with a poor prognosis. It is the third leading cause of cancer-related deaths within the United States, though it is on track to become the second…

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EA-2353 for Retinitis Pigmentosa (RP) Granted Fast Track Designation

Post author:Jessica Lynn
Post published:February 15, 2023
Post category:Retinitis pigmentosa

In the United States, Fast Track designation is granted to drugs designed to treat rare and/or serious conditions and that fill an unmet medical need. The process aims to…

Source: Pixabay

Scientists Discover Potential New Treatment for Alagille Syndrome

Post author:Jessica Lynn
Post published:February 6, 2023
Post category:Alagille Syndrome

Treatment for Alagille syndrome, a rare genetic disorder that affects multiple organ systems, are typically symptomatic. Many children born with this disorder eventually require a liver transplant; without this, Alagille…

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Could SGSH Enzyme Replacement Therapy Benefit Children with MPS III-A?

Post author:Jessica Lynn
Post published:February 3, 2023
Post category:MPS III MPS III (Sanfilippo Syndrome)Sanfilippo Syndrome

Enzyme replacement therapy (ERT) has been explored as a potential therapeutic option for mucopolysaccharidosis type III A (MPS III-A or Sanfilippo syndrome type A). However, these solutions have not…

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Anti-Hyperglycemic Medication Increases MS Risk in Adults with Type 2 Diabetes

Post author:Jessica Lynn
Post published:February 2, 2023
Post category:Multiple Sclerosis

Over the past few decades, research has shown a potential connection between metabolic disorders and multiple sclerosis (MS). While this connection has been made, anti-hyperglycemic medications (often used to…

Photo by Towfiqu barbhuiya on Unsplash

TP-3654 Shows Preliminary Benefits for Myelofibrosis

Post author:Jessica Lynn
Post published:February 2, 2023
Post category:Myelofibrosis

The American Society of Hematology (ASH) held its 64th Annual Meeting in December 2022, during which time a variety of medical stakeholders discussed issues, trends, and research in the…

Arcaion / Pixabay

ICYMI: Positive Topline Data Available on Pemvidutide for NAFLD

Post author:Jessica Lynn
Post published:February 1, 2023
Post category:Nonalcoholic fatty liver disease

In a late December 2022 news release from biopharmaceutical company Altimmune, Inc., the company shared that positive topline data was available from a 24-week study—including a 12-week extension—which evaluated…

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A Special Treatment Helped a Girl with Neuroblastoma

Post author:Jessica Lynn
Post published:January 31, 2023
Post category:Neuroblastoma

High-risk neuroblastoma can be difficult to treat in children. Some research suggests that between 40-50% of children with high-risk neuroblastoma relapse following treatment, causing poor outcomes. When Flora Gentleman was…

Found on: Unsplash

CZI Granted $1M to UNC Researchers to Study Necrotizing Enterocolitis

Post author:Jessica Lynn
Post published:January 26, 2023
Post category:Necrotizing enterocolitis

Prematurity and formula-feeding heighten the risk of necrotizing enterocolitis (NEC), a serious gastrointestinal issue. However, NEC is still poorly understood; in many cases, the exact cause is still unknown.…

mohamed_hassan / Pixabay

Phoenix Nest Launches Natural History Study of Sanfilippo Syndrome

Post author:Jessica Lynn
Post published:January 26, 2023
Post category:MPS III MPS III (Sanfilippo Syndrome)Sanfilippo Syndrome

Have you ever heard of a natural history study? In short, a natural history study studies people who have, or are at risk of developing, a specific medical condition;…

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Balancing CXCL5 Levels Could Potentially Treat Lupus

Post author:Jessica Lynn
Post published:January 25, 2023
Post category:Lupus

Currently, the standards-of-care for lupus include anti-malarial drugs such as hydroxychloroquine, corticosteroids and immune-suppressive therapies, and biologics such as Benlysta. But new therapies are urgently needed, especially as anywhere between…

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Man with MND Urges Others to Join Study

Post author:Jessica Lynn
Post published:January 24, 2023
Post category:Motor neuron disease

A few years ago, Dean Mooney began experiencing some troubling health symptoms. His left hand became stiff and sometimes difficult to use. Later, he developed a mild arm tremor. After…

Source: Pixabay.com

Second-Line Lenvima Could Prolong HCC Survival

Post author:Jessica Lynn
Post published:January 24, 2023
Post category:Hepatocellular Carcinoma

Despite medical advances and new therapeutic developments, hepatocellular carcinoma (HCC) remains difficult to treat; in part, this is due to the fact that HCC, like many liver cancers, is often…

https://pixabay.com/en/bioreactors-glass-anaerobic-chamber-1781344/

A Biosensor Could Improve Lip and Oral Cavity Cancer Diagnosis

Post author:Jessica Lynn
Post published:January 19, 2023
Post category:Lip and oral cavity cancer

In multiple disease states, early identification, diagnosis, and treatment can significantly improve overall survival rate and patient outcomes. This is especially true for lip and oral cavity cancer. According to…

qimono / Pixabay

Novel Rare Form of Progeria Identified in Malaysia

Post author:Jessica Lynn
Post published:January 11, 2023
Post category:Progeria

Initially, when doctors in Malaysia met with the 21-year-old patient, they suspected that he had mandibuloacral dysplasia. The man, 21 years old, was short in stature (3.8 ft tall)…

Raymond and Alex in 2022. Photo courtesy of Alex Gaudlap

A Ray of Sunshine: Alex Gaudlap’s Efforts to Raise Awareness of the Ultra-Rare VAMP2 (Pt. 2)

Post author:Jessica Lynn
Post published:January 6, 2023
Post category:Rare Disease

Before you read on, don't forget to check out Part 1 of our interview. In Part 1, Alex discusses the multi-year diagnostic odyssey to discover that Raymond has VAMP2. Today, we talk…

mattthewafflecat / Pixabay

Study Shows that Rituximab Improves GPA Remission

Post author:Jessica Lynn
Post published:January 5, 2023
Post category:Granulomatosis with Polyangiitis Vasculitis

Determining the safest, best, and most effective therapeutic options for patients is crucial to improving outcomes and ensuring optimal health. As shared in a story from MD Edge, researchers…

PublicDomainPictures / Pixabay

Research Explores Two Genes Linked to Microcephaly

Post author:Jessica Lynn
Post published:January 4, 2023
Post category:Microcephaly

As our understanding of genetics continues to grow, new gene variants are being identified and linked to the development of various diseases. According to Medical XPress, a research team from…

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Could “Cooling” Glioblastoma Improve Overall Survival?

Post author:Jessica Lynn
Post published:January 4, 2023
Post category:Glioblastoma

Unfortunately, the prognosis associated with glioblastoma is poor; some studies suggest that survival rates are 40% within one year of diagnosis and 17% within two years, with less than 7%…

qimono / Pixabay

Researchers Find Potential Congenital Hyperinsulinism Cause in Unexplored Genomic Region

Post author:Jessica Lynn
Post published:December 30, 2022
Post category:Congenital hyperinsulinism

There are a number of different forms of congenital hyperinsulinism, along with a variety of different causes: a mother’s unmanaged diabetes, premature birth, gene mutations. But up to half…

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Could Gut Bacteria Cause Colon Cancer in People with IBD?

Post author:Jessica Lynn
Post published:December 29, 2022
Post category:Inflammatory Bowel Disease

Prior studies have found a correlation between inflammatory bowel disease (IBD) and colorectal cancer; those with IBD are at an increased risk of developing this cancer compared to the…

OpenClipart-Vectors / Pixabay

Homosexual Men are 2x More Likely to Develop IBD, Study Says

Post author:Jessica Lynn
Post published:December 21, 2022
Post category:Crohn's disease Inflammatory Bowel Disease ulcerative Colitis

There are a number of risk factors associated with the development of inflammatory bowel disease (IBD). These include being younger in age, being Caucasian or of Ashkenazi Jewish descent,…

How Tonix is Working to Change the Prader-Willi Syndrome (PWS) Treatment Landscape: A Discussion with Dr. Seth Lederman

Early-Stage Ovarian Cancer Characterized by Microbe Colonization

New Genetic Test Could Aid Ovarian Cancer Care

Five-Year Survival Rate Rises for Pancreatic Cancer

EA-2353 for Retinitis Pigmentosa (RP) Granted Fast Track Designation

Scientists Discover Potential New Treatment for Alagille Syndrome

Could SGSH Enzyme Replacement Therapy Benefit Children with MPS III-A?

Anti-Hyperglycemic Medication Increases MS Risk in Adults with Type 2 Diabetes

TP-3654 Shows Preliminary Benefits for Myelofibrosis

ICYMI: Positive Topline Data Available on Pemvidutide for NAFLD

A Special Treatment Helped a Girl with Neuroblastoma

CZI Granted $1M to UNC Researchers to Study Necrotizing Enterocolitis

Phoenix Nest Launches Natural History Study of Sanfilippo Syndrome

Balancing CXCL5 Levels Could Potentially Treat Lupus

Man with MND Urges Others to Join Study

Second-Line Lenvima Could Prolong HCC Survival

A Biosensor Could Improve Lip and Oral Cavity Cancer Diagnosis

Novel Rare Form of Progeria Identified in Malaysia

A Ray of Sunshine: Alex Gaudlap’s Efforts to Raise Awareness of the Ultra-Rare VAMP2 (Pt. 2)

Study Shows that Rituximab Improves GPA Remission

Research Explores Two Genes Linked to Microcephaly

Could “Cooling” Glioblastoma Improve Overall Survival?

Researchers Find Potential Congenital Hyperinsulinism Cause in Unexplored Genomic Region

Could Gut Bacteria Cause Colon Cancer in People with IBD?

Homosexual Men are 2x More Likely to Develop IBD, Study Says

Why Your Voice in Research Matters: Groundbreaking Studies are Changing What's Possible

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The Let’s Chat CAR T One-on-One Mentor Program: Speaking with Someone Who Understands What You Are Going Through

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