Normally, amyotrophic lateral sclerosis (ALS), a progressive neurodegenerative disorder, affects individuals between ages 50-60, with prevalence increasing with age. Once diagnosed, patients typically survive for another 3-5 years. However,…
On May 24, 2021, biopharmaceutical company NeoImmuneTech, Inc. shared that the first patient was dosed in a pilot study centered around NT-I7 (efineptakin alfa). Altogether, the study is designed…
Over 50 years ago, levodopa was approved to treat patients with Parkinson's disease. To this day, levodopa, administered via pills or intravenously, remains the standard-of-care. But according to Parkinson's News…
A majority of individuals who have strokes are over the age of 60. But what happens when younger individuals have unexplained strokes? What causes these to happen? According to a…
During the American Society of Gene & Cell Therapy (ASGCT) 24th Annual Meeting, which took place virtually from May 11-14, 2021, biotechnology company M6P Therapeutics ("M6P") presented preclinical data…
Head and neck squamous cell carcinoma (SCC) is considered both aggressive and difficult to treat. In fact, doctors estimate that nearly 50% of all patients will eventually see the recurrence…
The CDC notes that in 2019, an estimated 409,000 people globally died of malaria - but a majority of those who died were children in sub-Saharan Africa. In fact, 94%…
There are multiple gene mutations associated with severe combined immunodeficiency (SCID), a rare genetic disorder which severely inhibits - or stops - immune function. But according to New Atlas, an…
From April 23-25, 2021, the American Academy of Dermatology (AAD) held its Virtual Meeting Experience (AAD VMX 2021). During the event, over 75 meetings discussed various research and other insights…
Currently, there are a number of potential treatment options for patients with multiple myeloma: immunomodulators, chemotherapy, HDAC inhibitors, steroids, and proteasome inhibitors. But according to Medical XPress, Peter Mac scientists…
According to Medical XPress, researchers from the Cerebrovascular Surgery and Interventions Center at Boston Children's Hospital recently developed a new test that can benefit patients with Moyamoya disease. This rare…
In many cases, therapies for patients with rare disease are first tested or developed in either 2D cell cultures or in animal models, such as fruit flies, mice, or zebrafish.…
Our livers play a huge role in our health. The liver regulates chemicals in the blood, filters toxins and wastes out of the body, breaks down fat, and even plays…
Nobody knew how much of an impact COVID-19 would have when it first appeared on the scene. Now, as of May 20, 2021, the novel coronavirus pandemic has led to…
The first time I got stung by a wasp, my knee swelled up to nearly 4x its size. While my allergy is more frustrating than fatal, I know that I…
Sometimes, in the midst of performing medical research, researchers may discover an association between two conditions. According to Lambert Eaton News, University of Turin researchers recently determined a link between…
This year, the American Academy of Neurology (AAN) Annual Meeting took place virtually from April 17-22, 2021. During the meeting, a variety of stakeholders discussed new treatments and research…
Currently, there is no cure for mesothelioma, and many treatment options revolve around surgery, radiation, or therapy. But could targeted treatment and precision oncology provide better patient outcomes? According to…
From April 23 to 25, 2021, the American Academy of Dermatology (AAD) held their 2021 Virtual Meeting Experience (AAD VMX 2021). During the meeting, a variety of dermatology stakeholders discussed…
Have you ever thought about whether measuring caffeine levels could give you insight into disease progression? Well according to Parkinson's News Today, researchers have discovered a potential link between…
Poly ADP ribose polymerase (PARP) inhibitors are targeted cancer therapies which block PARP, an enzyme. Normally, PARP plays a role in DNA repair. Thus, inhibiting PARP prevents cancer cells from…
There are two types of osteosarcoma, a rare bone cancer: localized or metastasized. If the cancer is localized, or in one area, the 5-year survival rate sits around 70-75%. However,…
In a recent news release, gene therapy company Taysha Gene Therapies ("Taysha") shared the publication of preclinical data on the company's drug candidate, TSHA-102. Currently, Taysha is exploring TSHA-102 as…
Clinical trial data offers immense insight into a drug's safety, efficacy, and tolerability. But it can also share how combining two treatments can impact patient outcomes or whether a…
Patient-reported and patient-driven registries can be crucial in understanding rare diseases or cancers, driving research, and forming communities. Now, according to a recent press release, a new registry is forming,…
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