According to a report by BioSpace, the United Kingdom’s National Institute’s of Health (NIH) recently diagnosed 31 conditions that were not previously recognized. The results date back to an initiative…
A clinical trial application for a Phase 1 study of the investigational drug KL1333 in healthy volunteers and patients with genetic mitochondrial diseases has been approved by a regulatory agency…
Death or Debt? That is the question that begins the title of a recent study that is examining "financial toxicity" for patients with newly diagnosed cancer. Treatment for cancer is…
According to a story from Endpoints News, the Chief Science Officer for Spark Therapeutics is close to finishing up his first year with the company. His name is Federico Mingozzi,…
According to a story from MD Magazine, researchers are using real-world studies, outside of the controls found in the clinical setting, to trace the impacts of multiple recently approved therapies…
According to a story from Compelo, the medical technology company LivaNova is kicking off an international trial that will assess the use of autonomic regulation therapy as a treatment for…
According to a report by the Canberra Times, a new clinical trial will present free genetic testing to ten thousand people. Each of these people is a potential parent. The…
Biogen Inc. has provided updates on their research into Spinraza® (nusinersen) in infants with spinal muscular atrophy. At the moment, Sprinraza is the only approved treatment for the condition. Data from…
Researchers have succeeded in editing genes to prevent a metabolic disorder called hereditary tyrosinemia type 1 (HT1) in animals while they are still in the womb. The team, who are…
According to a story from Reuters, a recent study found that mild exercise, such as walking, can significantly reduce the risk of heart failure in older, postmenopausal women. This large…
According to a story from Xcomony, the tech startup Glympse Bio has been developing a sensor technology that it claims will allow doctors to detect a variety of diseases earlier…
According to a story from prnewswire.co.uk, the biopharmaceutical company PTC Therapeutics recently announced the release of initial data from the first drug registry for its product Translarna (ataluren). This registry…
According to a story from MedicalXpress, a group of international scientists spearheaded by researchers at the University of Colorado have managed to identify certain genetic mutations that are connected to…
A team at the Research Institute of the McGill University Health Centre (RI-MUHC) in Canada is working to find a treatment for nephropathic cystinosis, a rare genetic disorder that affects…
According to a report by biopharmadive.com, Pfizer announced they will be dropping support for an experimental Duchenne muscular dystrophy treatment. The company intends to see if the treatment may be…
In order to improve the lives of patients for any illness, we all know research is an essential step. We also know that the most accurate research is derived from…
According to a report by CTV News, a number of clinics across Canada are offering an unproven treatment. These treatments focus on expensive and unverified stem cell therapies. The treatments…
According to a story from marketscreener.com, the drug development startup Endocyte has recently reached $1.5 billion in total value. This biopharmaceutical company has been focused on developing therapies for two…
A recent study conducted by PLOS Biology has revealed the importance of Active-DHA in the brain, particularly as it is still developing. This could mean big things in terms of…
HPV or human papillomavirus is the most common sexually transmitted disease in the US. It is so common that most sexually active people will catch the virus at some…
Researchers have previously found that patients with cancer who live in more rural locations have worse outcomes than those from urban places. However, it isn’t clear what causes this pattern.…
According to a story from PR-Inside, the biotechnology company Saniona recently announced that the second part of its Phase 2a clinical trial testing Tesomet as a treatment for Prader-Willi syndrome…
The United States Food and Drug Administration has awarded Fast Track designation to an investigational drug called PTG-300 for treating chronic anaemia caused by ineffective erythropoiesis in patients who have…
According to a story from HD Buzz, a recent study has conducted an in-depth investigation into juvenile onset Huntington's disease. It is quite unusual for this juvenile onset form to…
A study carried out by researchers from the University of North Carolina at Chapel Hill suggests that doctors in the state may not be testing patients for Ehrlichia infection often enough.…
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