Gene Therapy Takes a Giant Leap Forward
For many rare diseases, gene therapy, not traditional therapeutics, is perhaps the only means to significant relief and cure. However, the path to gene therapy has been strewn with obstacles…
For many rare diseases, gene therapy, not traditional therapeutics, is perhaps the only means to significant relief and cure. However, the path to gene therapy has been strewn with obstacles…
The 2019 Spastic Paraplegia Annual Conference Patients, their families, medical professionals, and caregivers are invited to attend this conference. Participants will have the opportunity to network with one another, build…
Robbie Edwards has a rare disease, one so rare that she's one of only 17 people in the world with it. She suffers from hereditary spastic paraplegia which represents a…