April 24, 2018 - Patient Worthy

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Anavex Plans to Trial its Treatment For Parkinson’s Disease Dementia, and Researchers are Hopeful that it Could Also Benefit Other Diseases

Post author:Anna Hewitt
Post published:April 24, 2018
Post category:Parkinson's Disease Rett Syndrome

A drug called Anavex 2-73 being developed to treat Parkinson’s disease dementia is planned to undergo testing in a Phase 2 clinical trial, reports Globe Newswire. Parkinson’s disease is a…

Source: Pixabay.com

$16 Million Donated to Childhood Cancer Research ‘Dream Team’

Post author:Anna Hewitt
Post published:April 24, 2018
Post category:Cancer Rare Disease

A team of childhood cancer researchers, known as the Pediatric Cancer Dream Team, were first created in 2013 through collaboration between the charitable organizations Stand Up To Cancer (SU2C)…

Source: Pixabay

A Common Virus is a Risk Factor for Seven Serious Diseases

Post author:Anna Hewitt
Post published:April 24, 2018
Post category:Juvenile idiopathic arthritis Multiple Sclerosis Rheumatoid Arthritis

A study carried out by researchers at Cincinnati Children’s Hospital has discovered that the extremely common Epstein-Barr virus is a risk factor for seven diseases, including lupus and multiple sclerosis.…

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Online Therapy Sets New Pace for Multiple Sclerosis Treatment

Post author:Samuel Sachs
Post published:April 24, 2018
Post category:Multiple Sclerosis

A new clinical study shows how the internet may provide opportunities for therapy. The study’s results detail how an online program called Elevida reduces fatigue in patients with multiple sclerosis.…

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April is Fabry Disease Awareness Month: Let’s Learn Something New Today!

Post author:Jean Martell
Post published:April 24, 2018
Post category:Fabry Disease Rare Disease

So what is Fabry disease you ask? You came to the right place! Fabry disease is a genetic, lysosomal storage disorder that occurs when a specific kind of fat known…

Source: Pixabay

A New Study Has Identified Why Patients With Hemophilia Have Such High Rates of Prosthetic Joint Infection and What Can be Done About It

Post author:Anna Hewitt
Post published:April 24, 2018
Post category:Hemophilia

The Orthopaedic Institute for Children (OIC) has found that improving the education of patients with hemophilia leads to a large reduction in rates of prosthetic joint infection, reports Bioportfolio.…

Source: Pixabay

Living with Hereditary Angiodema: My Life was Changed in an Instant, Part Two

Post author:Patient Worthy Contributor
Post published:April 24, 2018
Post category:HAE Hereditary Angiodema Rare Disease

Have you read part one of Loukisha's story? Check it out here! When I imagined life with my husband and children my plans didn’t include surgeries, walkers, canes, a wheelchair,…

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Hope for ALS Patients

Post author:Ellen Johnson
Post published:April 24, 2018
Post category:Amyotrophic Lateral Sclerosis

A clinical trial is ongoing to test if stem cells harvested from bone marrow and injected into an ALS (amyotrophic lateral sclerosis) patient's spinal fluid will stop or slow the…

Source: Pixabay

A Drug Trial for Phenylketonuria Has Dosed Its First Patient

Post author:Anna Hewitt
Post published:April 24, 2018
Post category:Phenylketonuria

A potential treatment for phenylketonuria has progressed to clinical trial stage and the first patient has been dosed, reports Business Wire. This follows successful trials of the drug in non-human…

Source: Pixabay

A Swine Model for Rare Disease Research Has Been Cleared by the FDA

Post author:Anna Hewitt
Post published:April 24, 2018
Post category:Ataxia-telangiectasia Rare Disease

The US Food and Drug Administration have just approved a genetically engineered swine research model for the rare disease ataxia telangiectasia for commercial use. The model, officially named the ExeGen…

Anavex Plans to Trial its Treatment For Parkinson’s Disease Dementia, and Researchers are Hopeful that it Could Also Benefit Other Diseases

$16 Million Donated to Childhood Cancer Research ‘Dream Team’

A Common Virus is a Risk Factor for Seven Serious Diseases

Online Therapy Sets New Pace for Multiple Sclerosis Treatment

April is Fabry Disease Awareness Month: Let’s Learn Something New Today!

A New Study Has Identified Why Patients With Hemophilia Have Such High Rates of Prosthetic Joint Infection and What Can be Done About It

Living with Hereditary Angiodema: My Life was Changed in an Instant, Part Two

Hope for ALS Patients

A Drug Trial for Phenylketonuria Has Dosed Its First Patient

A Swine Model for Rare Disease Research Has Been Cleared by the FDA

The Let’s Chat CAR T One-on-One Mentor Program: Speaking with Someone Who Understands What You Are Going Through

“Shades of Psoriasis”: Plaque Psoriasis and Sharing Your Story

Understanding RSV: Why Combatting Ethnic and Age-Related Health Disparities Could Improve Outcomes

We Need Equity and Diversity Within Rare Disease Research

DNA in Color: How Ronya Nelson is Working to Close the Diversity Gap in Genetics - Part 1

Bridging the Diversity Gap in Healthcare

Congratulations to the 2023 Recipients of the Diversity in Lupus Research Awards!

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