Happy end-of-June, readers! A lot of people are getting ready for the fourth of July right now. However, as a lot of the rare community knows, not everyone is able…
According to a story from news-medical.net, a team of scientists from Delaware have recently released a study in the journal BMC Bioinformatics. In this study, the researchers found that patters…
Researchers have been studying an experimental treatment for cystic fibrosis that is thought to be effective regardless of a patient's genetics. The research is still in the early stages, but…
My dysautonomia story starts around the year 2000, when I was 13 years old, though I never got a diagnosis until I was about 28! In the Fall of 2000, I…
According to a story from Reuters, the drug development company Merrimack Pharmaceuticals decided to abort its development of a new treatment for pancreatic cancer. The company chose to let go…
According to News Medical, a group of researchers at Johns Hopkins and the Bloomberg-Kimmel Institute for Cancer Immunotherapy recently found encouraging results for a study involving immunotherapy to treat a…
Amicus Therapeutics is developing a treatment for Pompe disease through its AT-GAA program. They have recently announced that they have met with regulators from the European Union and Germany who…
June is Apert Syndrome Awareness Month! As summer sets in, let's take a moment to learn a little more about this rare disease and do our part to raise some…
According to a story from globenewswire.com, the company Revive Therapeutics, which is dedicated to the development of treatments derived from cannabis and cannabinoids, recently announced that the FDA has decided…
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