A new neuromuscular research center has opened at the Ottawa Hospital. The new center will allow patients living with neuromuscular conditions, such as muscular dystrophy and ALS, to be a…
According to a story from PR-Inside, the biotechnology company Saniona recently announced that the second part of its Phase 2a clinical trial testing Tesomet as a treatment for Prader-Willi syndrome…
The United States Food and Drug Administration has awarded Fast Track designation to an investigational drug called PTG-300 for treating chronic anaemia caused by ineffective erythropoiesis in patients who have…
Rare diseases come in many forms, shapes, and sizes - with varying degrees of symptoms and attributes. Here is one that made news on the Internet, for it's peculiar and…
According to a story from HD Buzz, a recent study has conducted an in-depth investigation into juvenile onset Huntington's disease. It is quite unusual for this juvenile onset form to…
According to a story from The Atlantic, the continual development of gene editing technologies like CRISPR have the potential to cure a substantial portion of rare diseases that are linked…
According to a story from Scoop Independent News, speech therapists from the Waikato District in New Zealand have been using telehealth technology to great effect in order to deliver speech…
A study carried out by researchers from the University of North Carolina at Chapel Hill suggests that doctors in the state may not be testing patients for Ehrlichia infection often enough.…
LiPlaCis is a formulation of cisplatin that delivers its agent directly to cancerous tumor sites. Its efficacy has so far only been studied within breast cancer patients. However, scientists have reason to…
Actress Marcia Cross, best known for her role as Bree Van de Kamp on Desperate Housewives, has shared that she is now healthy after battling anal cancer in a series…
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