Results from a study that were presented at the European Society for Medical Oncology’s Congress have shown that the investigational drug for prostate cancer INO-5150 may be able to slow…
This is the second part of Amber's story. Check out part one here. June rolled around, and my appointment with the rheumatologist came up. The hour-long car ride there made…
According to a story from Markets Insider, the biotechnology company Innovate Biopharmaceuticals, Inc., recently announced encouraging proof-of-concept data for its lead medical product larazotide acetate. This experimental drug appears to…
According to a story from greeleytribune.com, a couple has been working to form a nonprofit to help spread awareness about an unusual rare disease called achalasia, which can cause the…
For esophageal cancer (like many rare conditions), early diagnosis means a better prognosis. Unfortunately, until now there haven't been many ways to determine whether or not an individual may be at…
November is Pancreatic Cancer Awareness Month. The American Cancer Society’s estimates for pancreatic cancer in the United States for 2018 are: About 55,440 people (29,200 men and 26,240 women) will…
A new study into a potential drug for cystic fibrosis has begun. The Phase Ib/IIa trial will investigate the drug POL6014 in up to forty patients who have cystic…
An innovative new treatment means practically nothing if we can't determine the type of patient it's going to be effective for. For an illness like acute myeloid leukemia (AML), which is…
A recent article titled ‘How I use molecular genetic tests to evaluate patients who have or may have myelodysplastic syndromes’ published in the journal Blood discusses the role of genetic testing for…
Hello all! My name is Amber Aerni. I am 28 years old, and I would like to tell you the story of my POTS journey. Yes, I refer to my…
According to a story from globenewswire.com, the drug developers Pfizer and Novartis have recently announced the beginning of a collaborative effort to test new potential therapies for nonalcoholic steatohepatitis (NASH).…
NSCLC Non-small cell lung cancer or NSCLC is the most common kind of lung cancer diagnosis. It affects over 2 million people and of those, there's a small group who…
An experimental therapy for melanoma patients has shown anti-tumour activity in an ongoing Phase 1 study. The therapy, called pegzilarginase (AEB1102) is being developed by Aeglea BioTherapeutics. For more…
According to a story from epidermolysisbullosanews.com, the biotechnology company TWi Biotechnology, Inc., recently announced that is has begun enrollment for its Phase 2 trial. This trial will test the company's…
Loxo Oncology has shared interim clinical data from an ongoing study of the drug LOXO-292. The study, a Phase 1/2 clinical trial, involves patients with RET-mutant medullary thyroid cancer, as…
A major genetic research project called the Deciphering Developmental Disorders (DDD) study is helping families to receive diagnoses, and, in some cases, even identifying new disorders. For more information,…
In a recent statement, Scott Gottlieb, the Commissioner of the US Food and Drug Administration, has re-affirmed the organisation’s commitment to modernising drug regulatory pathways. New changes are hoped to…
The problem Synapses in the brain are the connections between neurons that allow them to communicate with one another. In a healthy brain at least, that's how chemical signals are successfully…
According to a story from the Dartmouth Geisel School of Medicine, a group of researchers associated with the school recently published a study that indicated that certain scleroderma patients that…
According to a story from Cure Today, a recent study has found that identifying mutations in patients with myeloproliferative neoplasms may be the key in predicting outcomes, such as disease…
According to a story from mdmag.com, the publication recently conducted an interview with Dr. Eric Ruderman. Eric is a professor at Northwestern University with the Division of Rheumatology. The magazine…
Patients as Partners When you're diagnosed with an illness such as metastatic breast cancer, pancreatic cancer, or another rare disease that has limited treatment options, it's very easy to lose…
New data has been released about the effects of lenabasum, an experimental drug, on patients with systemic sclerosis and dermatomyositis. Corbus, who are developing lenabasum, are planning to present the…
Randy Hilliard, a doctor of psychiatry and University of Michigan professor, awards his survival to the privilege of being so close to a worldwide known cancer center and having the…
The cultural evolution of marijuana hit a new high when Canada recently legalized its recreational use, which also helped opened the door further to the medical exploration of marijuana's effectiveness.…
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