Kidney Disease Drug May Have Future Treating Mitochondrial Disorders
argzombies / Pixabay

Kidney Disease Drug May Have Future Treating Mitochondrial Disorders

A publication at Science Daily recently announced that findings from Children's Hospital of Philadelphia suggested that cysteamine bitartrate, already used for nephropathic cystinosis (a rare kidney disease), might potentially benefit patients…

Continue Reading Kidney Disease Drug May Have Future Treating Mitochondrial Disorders

New Resources Could Improve Drug Development for Fibrodysplasia Ossificans Progressiva

Ipsen has just announced that they will be acquiring Clementia Pharmaceuticals. This merging of companies is exciting for the rare community because it will strengthen the resources, knowledge-base, and overall…

Continue Reading New Resources Could Improve Drug Development for Fibrodysplasia Ossificans Progressiva
Theranexus Releases Early Data from its Narcolepsy Clinical Trial
PixelAnarchy / Pixabay

Theranexus Releases Early Data from its Narcolepsy Clinical Trial

According to a story from finanznachrichten.de, the biopharmaceutical company Theranexus has recently released preliminary results from a Phase II clinical trial that is testing the company's experimental product THN102. This…

Continue Reading Theranexus Releases Early Data from its Narcolepsy Clinical Trial
Study Finds That Clinical Costs for Orphan Drugs are Lower Than Costs for Non-Orphan Drugs
stevepb / Pixabay

Study Finds That Clinical Costs for Orphan Drugs are Lower Than Costs for Non-Orphan Drugs

According to a story from Regulatory Affairs Professionals Society, a recent study found that the research and development costs for new molecular entities that were classified as orphan drugs was…

Continue Reading Study Finds That Clinical Costs for Orphan Drugs are Lower Than Costs for Non-Orphan Drugs

FDA Releases New Info About How it Could Regulate Gene Therapy

According to a story from finance.yahoo.com, the US Food and Drug Administration (FDA) has recently released new guidelines that are related to how the agency will regulate and manage the…

Continue Reading FDA Releases New Info About How it Could Regulate Gene Therapy
Close Menu