Recently, a team of Yale researchers wanted to understand how genetic mutations in patients with Rett syndrome resulted in neurological issues. Using a unique type of genetic testing, researchers were…
This week, UbiVac and Bristol Myers Squibb announced their clinical trial collaboration in a Biospace press release. The two companies, in a Phase 1b trial, look to study whether combining…
In the geographically small island nation of New Zealand, there are estimated to be as many as 300,000 people who live with various rare diseases or disorders. Unfortunately, like in…
According to the ASCO Post, researchers have discovered genomic characteristics of smoldering multiple myeloma that can tell one's risk of progression to multiple myeloma. Dr. Mark Bustoros and his team…
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Summer is approaching, and Lyme disease is coming with it. Ticks and wildlife are more active in the warmer months, leading to an increase in tick-spread diseases. But because we…
According to a story from BioPharma Dive, the drug company Sarepta Therapeutics is pushing forward with its plans to develop a gene therapy for limb-girdle muscular dystrophy (LGMD). The company…
Myositis Myositis is an autoimmune disease that leads to muscle damage. Patients live with chronic disability due to the symptoms of this rare condition. These include skin rashes, pain, weakness, fatigue,…
June 17th is recognized as World CDKL5 Awareness Day and the month of June is considered CDKL5 Awareness Month. First organized by the International Foundation for CDKL5 Research (IFCR), the…
It is crazy to think back to a few months ago and see how much has changed. In March, SARS-CoV-2, which you probably know as COVID-19, was declared a global…
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