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Daily Archives: April 16, 2021

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Fecal Transplants Gave New Life to This Doctor with Recurrent C. Difficile Infections

Fecal Transplants Gave New Life to This Doctor with Recurrent C. Difficile Infections

  • Post author:Trudy Horsting
  • Post published:April 16, 2021
  • Post category:Rare Disease

C. difficile is a bacterial infection that impacts the gastrointestinal system. It can lead to weight loss, diarrhea, dehydration, and even the loss of blood platelets. Megan Newman has had…

Continue Reading Fecal Transplants Gave New Life to This Doctor with Recurrent C. Difficile Infections
Lizards and Lyme Disease: What’s the Connection?

Lizards and Lyme Disease: What’s the Connection?

  • Post author:Kendall Mason
  • Post published:April 16, 2021
  • Post category:Lyme Disease

Lyme disease is a vector-borne disease spread through ticks. It is most common in the Northeast, North-Central, and mid-Atlantic portions of the country, but is notably absent in the Southeast.…

Continue Reading Lizards and Lyme Disease: What’s the Connection?
Gum Bacteria Could Contribute to Alzheimer’s Disease
Source: Pixabay

Gum Bacteria Could Contribute to Alzheimer’s Disease

  • Post author:Jessica Lynn
  • Post published:April 16, 2021
  • Post category:Alzheimer's disease without Neurofibrillary tangles

Growing up, I was always told that oral health related directly to regular health. But now, a study from researchers at the NYU College of Dentistry and Weill Cornell Medicine…

Continue Reading Gum Bacteria Could Contribute to Alzheimer’s Disease
Sawyer’s Story: Community Support for Boy With Trifunctional Protein Deficiency

Sawyer’s Story: Community Support for Boy With Trifunctional Protein Deficiency

  • Post author:Kendall Mason
  • Post published:April 16, 2021
  • Post category:Rare Disease

Sawyer Burch is a four-year-old boy from the Nashville, Tennessee area who was born with trifunctional protein deficiency, a rare disorder that takes the body's ability to utilize certain types…

Continue Reading Sawyer’s Story: Community Support for Boy With Trifunctional Protein Deficiency
Clinical Trial for Gene Therapy for Krabbe Disease will Begin this Year

Clinical Trial for Gene Therapy for Krabbe Disease will Begin this Year

  • Post author:Trudy Horsting
  • Post published:April 16, 2021
  • Post category:Krabbe Disease

Passage Bio has recently announced that Orphan Drug Designation has been granted by the European Commission for PBKR03, a gene therapy for Krabbe Disease. This condition has yet to have…

Continue Reading Clinical Trial for Gene Therapy for Krabbe Disease will Begin this Year
GARDIAN Registry Launches for nGD Awareness
source: pixabay.com

GARDIAN Registry Launches for nGD Awareness

  • Post author:Jessica Lynn
  • Post published:April 16, 2021
  • Post category:Gaucher Disease/Gaucher disease type 3

In mid-April, Kantar Health and the International Gaucher Alliance (IGA) shared the launch of a rare disease registry developed by the partnership. The registry, known as GARDIAN, will explore Gaucher…

Continue Reading GARDIAN Registry Launches for nGD Awareness
Rare Classroom: Sickle Cell Disease
source: shutterstock

Rare Classroom: Sickle Cell Disease

  • Post author:James Moore
  • Post published:April 16, 2021
  • Post category:Sickle cell anemia/Sickle Cell Disease

Welcome to the Rare Classroom, a new series from Patient Worthy. Rare Classroom is designed for the curious reader who wants to get informed on some of the rarest, most…

Continue Reading Rare Classroom: Sickle Cell Disease
WP1066 for Ependymoma Earns Rare Pediatric Disease Designation
geralt / Pixabay

WP1066 for Ependymoma Earns Rare Pediatric Disease Designation

  • Post author:Jessica Lynn
  • Post published:April 16, 2021
  • Post category:Ependymoma

  Earlier this year, WP1066, a p-STAT3 inhibitor, received three separate Rare Pediatric Disease designations for the treatment of medulloblastoma, atypical teratoid rhabdoid tumor, and diffuse intrinsic pontine glioma. Now,…

Continue Reading WP1066 for Ependymoma Earns Rare Pediatric Disease Designation
Tocilizumab Shows Sustained Efficacy for Patients with GCA
multifacetedgirl / Pixabay

Tocilizumab Shows Sustained Efficacy for Patients with GCA

  • Post author:Jessica Lynn
  • Post published:April 16, 2021
  • Post category:Giant-cell arteritis/Vasculitis

Clinical trials can be beneficial in many ways. For one, these trials show researchers whether a treatment’s impact is durable and sustained. Determining this often requires some follow-up period. According…

Continue Reading Tocilizumab Shows Sustained Efficacy for Patients with GCA

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