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Daily Archives: September 16, 2022

Home » Archives for September 16, 2022
Study Shows Benefits of PXT3003 for CMT1A
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Study Shows Benefits of PXT3003 for CMT1A

  • Post author:Jessica Lynn
  • Post published:September 16, 2022
  • Post category:Charcot-Marie-Tooth disease

The Phase 3 PLEO-CMT clinical trial evaluated the safety, efficacy, and tolerability of PXT3003 for patients with Charcot-Marie-Tooth disease type 1A (CMT1A). Altogether, 323 people enrolled. During the trial, researchers…

Continue Reading Study Shows Benefits of PXT3003 for CMT1A
Community Supports Firefighter with GBS
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Community Supports Firefighter with GBS

  • Post author:Jessica Lynn
  • Post published:September 16, 2022
  • Post category:Guillain Barré syndrome/Guillain Barre Syndrome

Ryan Smith has always been tenacious in pursuing his goals. One of his most important goals? Supporting his family and his community. As a lieutenant with the Stillwater Fire Department,…

Continue Reading Community Supports Firefighter with GBS
ICYMI: Phone Clip-On Can Identify Zika Virus
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ICYMI: Phone Clip-On Can Identify Zika Virus

  • Post author:Jessica Lynn
  • Post published:September 16, 2022
  • Post category:Zika Virus

There are a number of different mosquito-borne illnesses. But sometimes it can be difficult to make an accurate diagnosis when these illnesses – and many others – share similar symptoms…

Continue Reading ICYMI: Phone Clip-On Can Identify Zika Virus

1st International Workshop on Myelodysplastic Syndromes Highlights

  • Post author:James Moore
  • Post published:September 16, 2022
  • Post category:Myelodysplastic syndromes

The 1st International Workshop on Myelodysplastic Syndromes was held this year in Miami, FL from June 24-26. This in-person event was a convergence of researchers and clinicians to discuss advances…

Continue Reading 1st International Workshop on Myelodysplastic Syndromes Highlights
Rare Classroom: Allan-Herndon-Dudley Syndrome
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Rare Classroom: Allan-Herndon-Dudley Syndrome

  • Post author:James Moore
  • Post published:September 16, 2022
  • Post category:Allan-Herndon-Dudley Syndrome

Welcome to the Rare Classroom, a new series from Patient Worthy. Rare Classroom is designed for the curious reader who wants to get informed on some of the rarest, most…

Continue Reading Rare Classroom: Allan-Herndon-Dudley Syndrome

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RARE CLASSROOM

Welcome to the Rare Classroom, a new series from Patient Worthy. Rare Classroom is designed for the curious reader who wants to get informed on some of the rarest, most mysterious diseases and conditions. This series is an opportunity to learn the basics about some of the diseases that almost no one hears much about.

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