According to a publication from Business Wire, the Israeli biotechnology company Minovia Therapeutics recently finished dosing the first participant in a phase I/II clinical study of the Company's experimental mitochondrial…
According to a publication at Markets Insider, the Food and Drug Administration (FDA) recently approved Soliris (eculizumab) as a treatment for neuromyelitis optica spectrum disorder. The approval marks the first…
According to a publication from the Oklahoma Nursing Times, Kenneth Wyatt celebrated his 80th birthday this past June 4th. The happy occasion also marked almost five months exactly since Wyatt…
According to a publication from WCAX, care providers at Children's Hospital Colorado are devising new ways to make life with eosinophilic esophagitis easier. One patient, six-year-old Eliana Yelpaala, is already…
According to a press release from BeiGene, the Company and SpringWorks Therapeutics have launched MapKure, LLC — a new, jointly-operated venture owned by both partners. MapKure was founded to develop…
According to a publication from Fabry Disease News, Russian researchers recently screened over five-and-a-half thousand patients for Fabry disease while they continued with prescribed hemodialysis. The researchers' study, published in…
According to a publication from the Basingstoke Gazette, a Basingstoke family is raising money for the children's hospice center that supported them through the loss of a child. Jessica and…
According to a publication from ANCA Vasculitis News, a recent Spanish study of over 100 individuals diagnosed with ANCA-associated vasculitis found that major infections are a main cause of death…
According to a publication from the Warwick Beacon, friends and family of 4-year-old Banner Mazza are raising money for the boy's medical expenses. Mazza was recently diagnosed with ROHHAD, a…
According to a press release from the Texas Biomedical Research Institute (Texas Biomed), researchers from the Institute have identified another new genetic mutation that they believe can cause rare congenital…
According to a press release from the Children's National Health System (a children's hospital in Washington, D.C.), two scientists from the Institution have been selected to receive federal funding grants…
According to a publication from EurekAlert, researchers from the University of Oklahoma College of Medicine (OUCM) recently published a study in the journal Gastroenterology suggesting how cachexia is triggered in…
According to a publication from the Arizona BioIndustry Association, Dr. Rachna Shroff and a team of researchers from the Arizona Cancer Center are studying the use of nab-paclitaxel (a pancreatic…
According to a publication from the BBC, researchers with King's College London believe they've identified early biomarkers for Parkinson's disease that could help physicians predict who will be affected up…
According to a press release from the California Institute for Regenerative Medicine (CIRM), the Institute's governing body has approved a grant of nearly $12 million to University of California, San…
According to a press release from the French biotechnology company Inventiva, the company has completed recruitment for a phase 2 clinical trial evaluating its experimental mucopolysaccharidosis VI drug, odiparcil. About…
According to a publication from Pharmaceutical Technology, California-based Eiger Biopharmaceuticals is preparing to submit a New Drug Application (NDA) to the Food and Drug Administration (FDA) for their experimental progeria…
According to a publication from Stat, researchers from the University of Michigan-led Genes for Good program have recruited over 20,000 Americans through its smartphone app. Participants complete questionnaires on the…
According to a publication from BioPortfolio, China's National Medical Products Administration (NMPA — similar to the American FDA) recently approved BioMarin's mucopolysaccharidosis type IVA drug Vimizim for use in the…
According to a publication from EurekAlert, a recent study helmed by the Royal Marsden NHS Foundation Trust suggests that female cancer patients tend to live slightly longer following treatment than…
According to a publication from Yahoo News, five doctors interviewed by the media organization have reported meeting with a number of migrants detained by United States Customs and Border Protection…
According to a publication from Medicine Matters, a 12-person task force organized by the European League Against Rheumatism (EULAR) has released a set of 12 recommendations to improve quality of…
According to a publication from Fierce Biotech, Biotech company Sangamo recently updated investors on three trials it has underway testing experimental forms of gene and cell therapies. The trials are…
According to a publication from Reuters, based on early clinical data, American biotechnology company BioMarin Pharmaceuticals believes that a single injection of its experimental hemophilia A drug could relieve symptoms…
According to a recent publication from BioPharma Dive, Dr. Janet Woodcock sat for an interview at the Biotechnology Innovation Organization's annual conference in Philadelphia earlier this month. Woodcock, the Director…
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