As reported in Forbes Magazine, sports have been upended in 2020, causing many athletes to miss their seasons debuts. Chris Archer, starting pitcher of the Pittsburgh Pirates, will be off…
As reported in Parkinson’s News Today, a new study has found that high blood levels of the antioxidant uric acid is correlated with heightened risk of developing levodopa-induced dyskinesia (LID)…
Arabel Standingbear sketches figures with lead pencils and paints realistic scenes with acrylics. Her poem was accepted by a museum. She has won in local art contests between schools, and…
In a story from Multiple Sclerosis News Today, multiple sclerosis is known for its variability- one patient's experience may look nothing like a friend's with the same disease. For this…
As reported in GSK, the FDA has just granted priority review to Nucala (mepolizumab), a targeted biological treatment to help patients with hypereosinophilic syndrome (HES). If the medication is accepted,…
As reported in QS Higher Education News, scientists at the Institute of Living Systems of the IKBFU and Kemerovo State University said they have improved a potential treatment option for PKU: the…
As reported in Parkinson's News Today; the way that COVID-19 interacts with pre-existing conditions is now being uncovered as the novel virus makes it way across the world. A new…
As reported in Guru Focus, biotech company Protagonist Therapeutics has announced progression in their Phase 2 study on PTG-300 as treatment for patients with polycythemia vera, a rare cancer. Dr.…
As reported in Multiple Sclerosis News Today, Jessie Ace tells the story of receiving her diagnosis with multiple sclerosis at 22. She wrote, "I hate needles." She ranks being told…
For Emma, the worst part of receiving her diagnosis with ankylosing spondylitis wasn't adapting to the constant pain, losing her breath over five minutes of standing, being too exhausted to…
In a story from MedCity News, while some studies grind to a halt with coronavirus restrictions, some of the medical world is using the new limitations to formulate creative solutions…
As reported in Med Gadget, Medtech company ’11 Health’ has made virtual healthcare affordable this quarantine season, providing patients with severe chronic digestive disorders 12 weeks of free access on their…
As reported in Vox, Amber Freed set into to motion when she learned her son Maxwell's genetic disorder made him just the 34th in the world to be diagnosed with…
As reported in Liverpool Echo; Faye was just 12 she began to have difficulty walking. She didn't realize it was her first encounter with the devastating disease that she had…
As reported in Medical Xpress, the U.S. Centers for Disease Control and Prevention have listed antibiotic resistance as one of the most pressing health challenges of our time. Infection treatment…
As reported by producer Minoryx; the pharmaceutical leriglitazone, used to treat early stage cerebral ALD (cALD) has just announced its plans to continue onto its Phase 2 Nexus trial without…
As reported in PressReleasePoint, Researchers at the University of Sheffield have found a clue to the cause of a set of rare neurological disorders known as leukodystrophies- an issue with…
The last decades have seen significant progress when it comes to medical care for rare diseases. Tasks doctors once slaved over were transformed with better speed and efficiency by modern…
As reported in WMS, Kathy Miska was beginning to have difficulty walking. This time, she knew what was happening. She'd seen the same thing happen to her sister, who went…
As reported in Dravet Syndrome News, in a new study, researchers created an artificial intelligence system which could diagnose epileptic conditions more rapidly and easily than existing systems. Epilepsy is…
As reported in Biospace, Adverum Biotechnologies, a gene therapy company focused on clinical stage trials for rare and ocular diseases with unmet needs, has successfully dosed a patient in their…
Brooke Ramirez's pregnancy with her first daughter went as planned, and her new baby Trinity passed her developmental milestones. It wasn't until she was five months old that they noticed…
As sourced from the Washington Post, COVID-19 coverage has been spreading the news: people with many disabilities are scared, and we need to take care of them. For many, the…
Alex Biagi was planning to try out for his high schools basketball team, and could already dunk. He said his dream was to be a professional basketball player. He grew…
As reported in Biospace, Fulcrum Therapeutics has announced it will be submitting an application to the FDA for FTX-6058 as an Investigational New Drug (IND) by the end of 2020…
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